Jones Charles H, Gollakota Akhila, Chen Mingfu, Chung Tai-Chun, Ravikrishnan Anitha, Zhang Guojian, Pfeifer Blaine A
Department of Chemical and Biological Engineering, University at Buffalo, The State University of New York, Buffalo, NY 14260-4200, USA.
Department of Chemical and Biological Engineering, University at Buffalo, The State University of New York, Buffalo, NY 14260-4200, USA.
Biomaterials. 2015 Jul;58:103-11. doi: 10.1016/j.biomaterials.2015.04.033. Epub 2015 May 11.
Given the rise of antibiotic resistant microbes, genetic vaccination is a promising prophylactic strategy that enables rapid design and manufacture. Facilitating this process is the choice of vector, which is often situationally-specific and limited in engineering capacity. Furthermore, these shortcomings are usually tied to an incomplete understanding of the structure-function relationships driving vector-mediated gene delivery. Building upon our initial report of a hybrid bacterial-biomaterial gene delivery vector, a comprehensive structure-function assessment was completed using a class of mannosylated poly(beta-amino esters). Through a top-down screening methodology, an ideal polymer was selected on the basis of gene delivery efficacy and then used for the synthesis of a stratified molecular weight polymer library. By eliminating contributions of polymer chemical background, we were able to complete an in-depth assessment of gene delivery as a function of (1) polymer molecular weight, (2) relative mannose content, (3) polymer-membrane biophysical properties, (4) APC uptake specificity, and (5) serum inhibition. In summary, the flexibility and potential of the hybrid design featured in this work highlights the ability to systematically probe vector-associated properties for the development of translational gene delivery candidates.
鉴于抗生素耐药微生物的增加,基因疫苗接种是一种有前景的预防策略,能够实现快速设计和制造。促进这一过程的是载体的选择,载体通常因情况而异且工程能力有限。此外,这些缺点通常与对驱动载体介导的基因传递的结构-功能关系的不完全理解有关。基于我们最初关于混合细菌-生物材料基因传递载体的报告,使用一类甘露糖基化聚(β-氨基酯)完成了全面的结构-功能评估。通过自上而下的筛选方法,基于基因传递效率选择了一种理想的聚合物,然后用于合成分层分子量聚合物文库。通过消除聚合物化学背景的影响,我们能够深入评估基因传递与以下因素的关系:(1)聚合物分子量,(2)相对甘露糖含量,(3)聚合物-膜生物物理性质,(4)抗原呈递细胞摄取特异性,以及(5)血清抑制。总之,这项工作中混合设计的灵活性和潜力突出了系统探究载体相关特性以开发转化型基因传递候选物的能力。