罕见肺部疾病与孤儿药：我们现状如何，又将何去何从？
Rare pulmonary diseases and orphan drugs: where do we stand and where are we going to?
作者信息
Harari Sergio, Humbert Marc, Blasi Francesco, Collard Harold R, Matucci-Cerinic Marco, Simonneau Gerald, Vancheri Carlo, Wells Athol U, Cottin Vincent
机构信息
U.O. di Pneumologia e Terapia Semi-Intensiva Respiratoria, Servizio di Fisiopatologia Respiratoria ed Emodinamica Polmonare, Ospedale San Giuseppe, MultiMedica IRCCS, Milan, Italy
Univ. Paris-Sud, Faculté de Médecine, Le Kremlin-Bicêtre, France AP-HP, Centre de Référence de l'Hypertension Pulmonaire Sévère, Département Hospitalo-Universitaire (DHU) Thorax Innovation (TORINO), Service de Pneumologie, Hôpital de Bicêtre, Le Kremlin-Bicêtre, France UMR_S 999, Univ. Paris-Sud, INSERM, Laboratoire d'Excellence (LabEx) en Recherche sur le Médicament et l'Innovation Thérapeutique (LERMIT), Centre Chirurgical Marie Lannelongue, Le Plessis-Robinson, France.
出版信息
Eur Respir Rev. 2015 Sep;24(137):375-7. doi: 10.1183/16000617.0051-2015.
Abstract
摘要
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