Jelsig Anne Marie, Brusgaard Klaus, Hansen Tine Plato, Qvist Niels, Larsen Martin, Bojesen Anders, Nielsen Claus Buhl, Ousager Lilian Bomme
a Department of Clinical Genetics , Odense University Hospital , Odense C , Denmark ;
b Institute of Clinical Research, University of Southern Denmark , Odense C , Denmark ;
Scand J Gastroenterol. 2016 Sep;51(9):1118-25. doi: 10.1080/00365521.2016.1174880. Epub 2016 May 5.
A subgroup of patients with hamartomatous polyps in the GI tract has a hereditary Hamartomatous Polyposis Syndrome with an increased risk of cancer. The distinction between patients with one or few polyps and patients with a syndrome can be difficult. A pathogenic germline mutation can be detected in a majority of HPS patients. This study investigates whether patients with one or few hamartomatous polyps could have a syndrome based on genetic screening of relevant genes.
We designed a gene panel including 26 hamartomatous polyposis-associated genes. Using targeted Next Generation Sequencing, DNA samples from 77 patients with 84 hamartomatous polyps were sequenced. The detected germline variants were classified into pathogenicity classes.
We detected several germline variants, among them three in ENG, two in BMPR1A, one in PTEN, and one in SMAD4. Although some of the detected variants have been reported previously none could be definitely pathogenic or likely pathogenic.
Our study points towards that genetic testing for the Hamartomatous Polyposis Syndromes in patients with one or few polyps does not improve diagnostics, however we illustrate that the clinical significance of genetic variants can be difficult to interpret. A family history of polyps, cancer, or extraintestinal findings or a minimum of 3-5 polyps seems to be relevant information to include before genetic testing.
胃肠道错构瘤性息肉患者的一个亚组患有遗传性错构瘤性息肉综合征,癌症风险增加。区分有一个或几个息肉的患者和患有综合征的患者可能很困难。大多数遗传性息肉综合征(HPS)患者可检测到致病种系突变。本研究基于对相关基因的基因筛查,调查有一个或几个错构瘤性息肉的患者是否可能患有综合征。
我们设计了一个包含26个错构瘤性息肉相关基因的基因检测板。使用靶向新一代测序技术,对77例患有84个错构瘤性息肉的患者的DNA样本进行测序。将检测到的种系变异分类为致病性类别。
我们检测到几个种系变异,其中ENG基因有三个,BMPR1A基因有两个,PTEN基因有一个,SMAD4基因有一个。尽管之前已经报道过一些检测到的变异,但没有一个可以确定为致病性或可能致病性。
我们的研究表明,对有一个或几个息肉的患者进行遗传性息肉综合征的基因检测并不能改善诊断,然而我们表明基因变异的临床意义可能难以解释。息肉、癌症或肠外表现的家族史或至少3 - 5个息肉似乎是基因检测前需要纳入的相关信息。