Kessler Pascal, Marchot Pascale, Silva Marcela, Servent Denis
Service d'Ingénierie Moléculaire des Protéines (SIMOPRO), IBITECS, CEA, Université Paris-Saclay, Gif-sur-Yvette, France.
Aix-Marseille Université/Centre National de la Recherche Scientifique, Architecture et Fonction des Macromolécules Biologiques laboratory, Faculté des Sciences Campus Luminy, Marseille, France.
J Neurochem. 2017 Aug;142 Suppl 2:7-18. doi: 10.1111/jnc.13975. Epub 2017 Mar 21.
Three-finger fold toxins are miniproteins frequently found in Elapidae snake venoms. This fold is characterized by three distinct loops rich in β-strands and emerging from a dense, globular core reticulated by four highly conserved disulfide bridges. The number and diversity of receptors, channels, and enzymes identified as targets of three-finger fold toxins is increasing continuously. Such manifold diversity highlights the specific adaptability of this fold for generating pleiotropic functions. Although this toxin superfamily disturbs many biological functions by interacting with a large diversity of molecular targets, the most significant target is the cholinergic system. By blocking the activity of the nicotinic and muscarinic acetylcholine receptors or by inhibiting the enzyme acetylcholinesterase, three-finger fold toxins interfere most drastically with neuromuscular junction functioning. Several of these toxins have become powerful pharmacological tools for studying the function and structure of their molecular targets. Most importantly, since dysfunction of these receptors/enzyme is involved in many diseases, exploiting the three-finger scaffold to create novel, highly specific therapeutic agents may represent a major future endeavor. This is an article for the special issue XVth International Symposium on Cholinergic Mechanisms.
三指折叠毒素是在眼镜蛇科蛇毒中经常发现的微型蛋白质。这种折叠结构的特点是有三个不同的富含β链的环,从由四个高度保守的二硫键构成的致密球状核心中伸出。被确定为三指折叠毒素靶点的受体、通道和酶的数量及多样性在不断增加。这种多样的多样性突出了这种折叠结构在产生多效性功能方面的特定适应性。尽管这个毒素超家族通过与多种分子靶点相互作用干扰了许多生物学功能,但最重要的靶点是胆碱能系统。通过阻断烟碱型和毒蕈碱型乙酰胆碱受体的活性或抑制乙酰胆碱酯酶,三指折叠毒素对神经肌肉接头功能的干扰最为严重。其中几种毒素已成为研究其分子靶点功能和结构的强大药理学工具。最重要的是,由于这些受体/酶的功能障碍与许多疾病有关,利用三指支架来开发新型、高度特异性的治疗药物可能是未来的一项主要工作。这是一篇发表于第十五届国际胆碱能机制研讨会特刊的文章。