Southwood Cherie M, Garshott Danielle M, Richardson Chelsea R, Seraji-Bozorgzad Navid, Fribley Andrew M, Gow Alexander
Center for Molecular Medicine and Genetics, Wayne State University School of Medicine, Detroit, MI, USA.
Carman and Ann Adams Department of Pediatrics, Wayne State University School of Medicine, Detroit, MI, USA.
J Neurochem. 2017 Jul;142(1):103-117. doi: 10.1111/jnc.14035. Epub 2017 May 3.
Multiple sclerosis (MS) is considered a primary autoimmune disease; however, this view is increasingly being challenged in basic and clinical science arenas because of the growing body of clinical trials' data showing that exclusion of immune cells from the CNS only modestly slows disease progression to disability. Accordingly, there is significant need for expanding the scope of potential disease mechanisms to understand the etiology of MS. Concomitantly, the use of a broader range of pre-clinical animal models for characterizing existing efficacious clinical treatments may elucidate additional or unexpected mechanisms of action for these drugs that augment insight into MS etiology. Herein, we explore the in vivo mechanism of action of dimethyl fumarate, which has been shown to suppress oxidative stress and immune cell responses in psoriasis and MS. Rather than studying this compound in the context of an experimental autoimmune-induced attack on the CNS, we have used a genetic model of hypomyelination, male rumpshaker (rsh) mice, which exhibit oligodendrocyte metabolic stress and startle-induced subcortical myoclonus during development and into adulthood. We find that myoclonus is reduced 30-50% in treated mutants but we do not detect substantial changes in metabolic or oxidative stress response pathways, cytokine modulation, or myelin thickness (assessed by anova). All procedures involving vertebrate animals in this study were reviewed and approved by the IACUC committee at Wayne State University.
多发性硬化症(MS)被认为是一种原发性自身免疫性疾病;然而,由于越来越多的临床试验数据表明,将免疫细胞排除在中枢神经系统之外仅能适度减缓疾病向残疾的进展,这一观点在基础科学和临床科学领域正日益受到挑战。因此,迫切需要扩大潜在疾病机制的范围,以了解MS的病因。与此同时,使用更广泛的临床前动物模型来表征现有的有效临床治疗方法,可能会阐明这些药物的其他或意想不到的作用机制,从而加深对MS病因的理解。在此,我们探讨了富马酸二甲酯的体内作用机制,该药物已被证明可抑制银屑病和MS中的氧化应激和免疫细胞反应。我们没有在实验性自身免疫诱导的对中枢神经系统攻击的背景下研究这种化合物,而是使用了一种髓鞘形成不足的遗传模型,即雄性摇尾小鼠(rsh),这些小鼠在发育过程中及成年后表现出少突胶质细胞代谢应激和惊吓诱导的皮质下肌阵挛。我们发现,在接受治疗的突变体中,肌阵挛减少了30 - 50%,但我们没有检测到代谢或氧化应激反应途径、细胞因子调节或髓鞘厚度(通过方差分析评估)有实质性变化。本研究中涉及脊椎动物的所有程序均经过韦恩州立大学IACUC委员会的审查和批准。