Mikami Satoshi, Kawasaki Masanori, Ikeda Shuhei, Negoro Nobuyuki, Nakamura Shinji, Nomura Izumi, Ashizawa Tomoko, Kokubo Hironori, Hoffman Isaac Dylan, Zou Hua, Oki Hideyuki, Uchiyama Noriko, Hiura Yuuto, Miyamoto Maki, Itou Yuuki, Nakashima Masato, Iwashita Hiroki, Taniguchi Takahiko
Pharmaceutical Research Division, Takeda Pharmaceutical Company, Limited.
Takeda California, Inc.
Chem Pharm Bull (Tokyo). 2017;65(11):1058-1077. doi: 10.1248/cpb.c17-00564.
It has been hypothesized that selective inhibition of phosphodiesterase (PDE) 2A could potentially be a novel approach to treat cognitive impairment in neuropsychiatric and neurodegenerative disorders through augmentation of cyclic nucleotide signaling pathways in brain regions associated with learning and memory. Following our earlier work, this article describes a drug design strategy for a new series of lead compounds structurally distinct from our clinical candidate 2 (TAK-915), and subsequent medicinal chemistry efforts to optimize potency, selectivity over other PDE families, and other preclinical properties including in vitro phototoxicity and in vivo rat plasma clearance. These efforts resulted in the discovery of N-((1S)-2-hydroxy-2-methyl-1-(4-(trifluoromethoxy)phenyl)propyl)-6-methyl-5-(3-methyl-1H-1,2,4-triazol-1-yl)pyrazolo[1,5-a]pyrimidine-3-carboxamide (20), which robustly increased 3',5'-cyclic guanosine monophosphate (cGMP) levels in the rat brain following an oral dose, and moreover, attenuated MK-801-induced episodic memory deficits in a passive avoidance task in rats. These data provide further support to the potential therapeutic utility of PDE2A inhibitors in enhancing cognitive performance.
据推测,选择性抑制磷酸二酯酶(PDE)2A可能是一种治疗神经精神疾病和神经退行性疾病中认知障碍的新方法,其通过增强与学习和记忆相关脑区的环核苷酸信号通路来实现。继我们早期的工作之后,本文描述了一种针对一系列新型先导化合物的药物设计策略,这些化合物在结构上与我们的临床候选药物2(TAK - 915)不同,随后进行了药物化学研究以优化其效力、对其他PDE家族的选择性以及其他临床前特性,包括体外光毒性和体内大鼠血浆清除率。这些研究工作导致发现了N - ((1S)-2 - 羟基 - 2 - 甲基 - 1 - (4 - (三氟甲氧基)苯基)丙基)-6 - 甲基 - 5 - (3 - 甲基 - 1H - 1,2,4 - 三唑 - 1 - 基)吡唑并[1,5 - a]嘧啶 - 3 - 甲酰胺(20),口服给药后该化合物能显著提高大鼠脑中3',5'-环鸟苷单磷酸(cGMP)水平,此外,在大鼠被动回避任务中能减轻MK - 801诱导的情景记忆缺陷。这些数据进一步支持了PDE2A抑制剂在增强认知表现方面的潜在治疗效用。