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Infantile Pompe Disease and Enzyme Replacement Therapy.

作者信息

Amdani Shahnawaz M, Sanil Yamuna

机构信息

Division of Pediatric Cardiology, St. Louis Children's Hospital, Washington University School of Medicine, St. Louis, Missouri, United States.

Division of Cardiology, The Carman and Ann Adams Department of Pediatrics, The Children's Hospital of Michigan, Wayne State University School of Medicine, Detroit, Michigan, United States.

出版信息

J Paediatr Child Health. 2017 Dec;53(12):1242-1243. doi: 10.1111/jpc.13733.

DOI:10.1111/jpc.13733
PMID:29205646
Abstract
摘要

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