Therapy for Spinal Muscular Atrophy.
作者信息
Mendell Jerry R
机构信息
Nationwide Children’s Hospital, Columbus, OH
出版信息
N Engl J Med. 2018 Feb 1;378(5):487. doi: 10.1056/NEJMc1715769.
PMID:29394473
Abstract
摘要
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