Oligonucleotide Drugs for Transthyretin Amyloidosis.
作者信息
Buxbaum Joel N
机构信息
Scripps Research Institute, La Jolla, CA
出版信息
N Engl J Med. 2018 Nov 22;379(21):2086. doi: 10.1056/NEJMc1810994.
PMID:30462941
Abstract
摘要
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