PlantVax Corporation, Rockville, Maryland United States of America.
Institute of Human Virology, University of Maryland School of Medicine, Baltimore, Maryland, United States of America.
PLoS One. 2019 Feb 20;14(2):e0212649. doi: 10.1371/journal.pone.0212649. eCollection 2019.
Recombinant antibodies play increasingly important roles as immunotherapeutic treatments for human cancers as well as inflammatory and infectious diseases and have revolutionized their management. In addition, their therapeutic potential may be enhanced by the introduction of defined mutations in the crystallizable fragment (Fc) domains eg YTE (M252Y/S254T/T256E) and LS (M428L/N434S), as a consequence of increased half-lives and prolonged duration of protection. However, the functional properties of any biologic may be compromised by unanticipated immunogenicity in humans, rendering them ineffective. Several potent broadly neutralizing HIV monoclonal antibodies (bnAbs) have been identified that protect against SHIV challenge in macaque models and reduce HIV viremia in HIV-infected individuals. In the present study, the pharmacokinetics and immunogenicity of one or more 5mg/kg subcutaneous (SC) injections in naïve macaques of the HIV bnAb PGT121 and its PGT121-YTE mutant, both produced in plants, have been compared towards prolonging efficacy. Induction of anti-drug/anti-idiotypic antibodies (ADA, anti-id) has been monitored using both binding ELISAs and more functional inhibition of virus neutralization (ID50) assays. Timing of the anti-Id responses and their impact on pharmacokinetic profiles (clearance) and efficacy (protection) have also been assessed. The results indicate that ADA induction in naïve macaques may result both from injection of the previously non-immunogenic PGT121 into pre-primed animals and also by the introduction of the YTE mutation. Binding ADA antibody levels, induced in 7/10 macaques within two weeks of a first or second PGT121-YTE injection, were closely associated with both reduced pharmacokinetic profiles and loss of protection. However no correlation was observed with inhibitory ADA activity. These studies provide insights into both the structural features of bnAb and the immune status of the host which may contribute to the development of ADA in macaques and describe possible YTE-mediated changes in structure/orientation of HIV bnAbs that trigger such responses.
重组抗体在人类癌症、炎症和传染病的免疫治疗中发挥着越来越重要的作用,并彻底改变了这些疾病的治疗方式。此外,通过在可结晶片段(Fc)结构域中引入特定突变,如 YTE(M252Y/S254T/T256E)和 LS(M428L/N434S),可以增强其治疗潜力,从而延长半衰期和保护时间。然而,任何生物制剂的功能特性都可能因在人类中出现意外的免疫原性而受到损害,导致其无效。已经鉴定出几种有效的广谱中和 HIV 单克隆抗体(bnAbs),它们可以保护猕猴模型免受 SHIV 攻击,并降低 HIV 感染者的 HIV 病毒载量。在本研究中,比较了在 naive 猕猴中皮下(SC)注射一次或多次 5mg/kg 的 PGT121 及其在植物中产生的 PGT121-YTE 突变体的药代动力学和免疫原性,以延长疗效。使用结合 ELISA 和更具功能性的病毒中和抑制(ID50)测定法监测抗药物/抗独特型抗体(ADA,抗 id)的诱导。还评估了抗独特型反应的时间及其对药代动力学谱(清除率)和疗效(保护)的影响。结果表明,在 naive 猕猴中诱导 ADA 可能是由于将以前非免疫原性的 PGT121 注射到预先致敏的动物中,以及引入 YTE 突变所致。在首次或第二次 PGT121-YTE 注射后两周内,10 只猕猴中有 7 只诱导出结合 ADA 抗体水平,与降低药代动力学谱和丧失保护作用密切相关。然而,与抑制性 ADA 活性没有观察到相关性。这些研究提供了关于 bnAb 的结构特征和宿主免疫状态的见解,这些见解可能有助于在猕猴中产生 ADA,并描述了可能导致这种反应的 HIV bnAb 的 YTE 介导的结构/取向变化。