Ashaie Maeirah Afzal, Islam Rowshan Ara, Kamaruzman Nur Izyani, Ibnat Nabilah, Tha Kyi Kyi, Chowdhury Ezharul Hoque
Jeffrey Cheah School of Medicine and Health Sciences, Monash University Malaysia, Jalan Lagoon Selatan, Bandar Sunway, Subang Jaya 47500, Malaysia.
Health & Wellbeing Cluster, Global Asia in the 21st Century (GA21) Platform, Monash University Malaysia, Jalan Lagoon Selatan, Bandar Sunway, Subang Jaya 47500, Malaysia.
Pharmaceutics. 2019 Jul 2;11(7):309. doi: 10.3390/pharmaceutics11070309.
While several treatment strategies are applied to cure breast cancer, it still remains one of the leading causes of female deaths worldwide. Since chemotherapeutic drugs have severe side effects and are responsible for development of drug resistance in cancer cells, gene therapy is now considered as one of the promising options to address the current treatment limitations. Identification of the over-expressed genes accounting for constitutive activation of certain pathways, and their subsequent knockdown with specific small interfering RNAs (siRNAs), could be a powerful tool in inhibiting proliferation and survival of cancer cells. In this study, we delivered siRNAs against mRNA transcripts of over-regulated cell adhesion molecules such as catenin alpha 1 (CTNNA1), catenin beta 1 (CTNNB1), talin-1 (TLN1), vinculin (VCL), paxillin (PXN), and actinin-1 (ACTN1) in human (MCF-7 and MDA-MB-231) and murine (4T1) cell lines as well as in the murine female Balb/c mice model. In order to overcome the barriers of cell permeability and nuclease-mediated degradation, the pH-sensitive carbonate apatite (CA) nanocarrier was used as a delivery vehicle. While targeting CTNNA1, CTNNB1, TLN1, VCL, PXN, and ACTN1 resulted in a reduction of cell viability in MCF-7 and MDA-MB-231 cells, delivery of all these siRNAs via carbonate apatite (CA) nanoparticles successfully reduced the cell viability in 4T1 cells. In 4T1 cells, delivery of CTNNA1, CTNNB1, TLN1, VCL, PXN, and ACTN1 siRNAs with CA caused significant reduction in phosphorylated and total AKT levels. Furthermore, reduced band intensity was observed for phosphorylated and total MAPK upon transfection of 4T1 cells with CTNNA1, CTNNB1, and VCL siRNAs. Intravenous delivery of CTNNA1 siRNA with CA nanoparticles significantly reduced tumor volume in the initial phase of the study, while siRNAs targeting CTNNB1, TLN1, VCL, PXN, and ACTN1 genes significantly decreased the tumor burden at all time points. The tumor weights at the end of the treatments were also notably smaller compared to CA. This successfully demonstrates that targeting these dysregulated genes via RNAi and by using a suitable delivery vehicle such as CA could serve as a promising therapeutic treatment modality for breast cancers.
尽管有多种治疗策略用于治疗乳腺癌,但它仍是全球女性死亡的主要原因之一。由于化疗药物有严重的副作用且会导致癌细胞产生耐药性,基因治疗现在被认为是解决当前治疗局限性的有前景的选择之一。鉴定导致某些通路组成性激活的过表达基因,并随后用特异性小干扰RNA(siRNA)将其敲低,可能是抑制癌细胞增殖和存活的有力工具。在本研究中,我们将针对细胞粘附分子如连环蛋白α1(CTNNA1)、连环蛋白β1(CTNNB1)、踝蛋白-1(TLN1)、纽蛋白(VCL)、桩蛋白(PXN)和辅肌动蛋白-1(ACTN1)等过表达的mRNA转录本的siRNA递送至人(MCF-7和MDA-MB-231)和小鼠(4T1)细胞系以及雌性Balb/c小鼠模型中。为了克服细胞通透性和核酸酶介导的降解障碍,使用了pH敏感的碳酸磷灰石(CA)纳米载体作为递送工具。虽然靶向CTNNA1、CTNNB1、TLN1、VCL、PXN和ACTN1导致MCF-7和MDA-MB-231细胞的细胞活力降低,但通过碳酸磷灰石(CA)纳米颗粒递送所有这些siRNA成功降低了4T1细胞的细胞活力。在4T1细胞中,用CA递送CTNNA1、CTNNB1、TLN1、VCL、PXN和ACTN1的siRNA导致磷酸化和总AKT水平显著降低。此外,在用CTNNA1、CTNNB1和VCL的siRNA转染4T1细胞后,观察到磷酸化和总MAPK的条带强度降低。在研究初期,用CA纳米颗粒静脉递送CTNNA1的siRNA显著减小了肿瘤体积,而靶向CTNNB1、TLN1、VCL、PXN和ACTN1基因的siRNA在所有时间点均显著降低了肿瘤负荷。与CA相比,治疗结束时的肿瘤重量也明显更小。这成功证明了通过RNA干扰并使用合适的递送载体如CA靶向这些失调基因可作为一种有前景的乳腺癌治疗方式。