Tel Aviv Medical Center and Sackler Faculty of Medicine, Tel Aviv, Israel.
Department of Hematology, Jagiellonian University Medical College, Cracow, Poland.
Am J Hematol. 2019 Oct;94(10):1132-1140. doi: 10.1002/ajh.25579. Epub 2019 Aug 13.
The current study assesses the characteristics and outcomes of multiple myeloma (MM) patients, treated with novel agents for hematogenous extramedullary (HEMM) relapse. Consecutive patients diagnosed with HEMM between 2010-2018 were included. Patients' characteristics at diagnosis and at HEMM presentation, response to treatment, survival and factors predicting survival were recorded and analyzed. A group of 127 patients, all diagnosed with HEMM by imaging (87.3%) and/or biopsy (79%), were included. Of those, 44% were initially diagnosed with ISS3, 57% presented with plasmacytomas, and 30% had high-risk cytogenetics. Median time to HEMM was 32 months. In multivariate analysis, ISS3 and bone plasmacytoma predicted shorter time to HEMM (P = .005 and P = .008, respectively). Upfront autograft was associated with longer time to HEMM (P = .002). At HEMM, 32% of patients had no BM plasmacytosis, 20% had non-secretory disease and 43% had light-chain disease. Multiple HEMM sites were reported in 52% of patients, mostly involving soft tissue, skin (29%), and pleura/lung (25%). First treatment for HEMM included proteasome inhibitors (50%), immunomodulatory drugs (IMiDs) (39%), monoclonal antibodies (10%), and chemotherapy (53%). Overall response rate (ORR) was 57%. IMiDs were associated with higher ORR (HR 2.2, 95% CI 1.02-4.7, P = .04). Median survival from HEMM was 6 months (CI 95% 4.8-7.2). Failure to achieve ≥VGPR was the only significant factor for worse OS in multivariate analyses (HR = 9.87, CI 95% 2.35 - 39, P = .001). In conclusion, HEMM occurs within 3 years of initial myeloma diagnosis and is associated with dismal outcome. The IMiDs might provide a higher response rate, and achievement of ≥VGPR predicts longer survival.
本研究评估了接受新型血液外髓(HEMM)复发治疗的多发性骨髓瘤(MM)患者的特征和结局。纳入了 2010 年至 2018 年间诊断为 HEMM 的连续患者。记录和分析了患者在诊断时和 HEMM 表现时的特征、对治疗的反应、生存情况以及预测生存的因素。共纳入 127 例患者,所有患者均通过影像学(87.3%)和/或活检(79%)诊断为 HEMM。其中,44%的患者最初被诊断为 ISS3,57%的患者表现为浆细胞瘤,30%的患者具有高危细胞遗传学特征。中位至 HEMM 的时间为 32 个月。多变量分析显示,ISS3 和骨浆细胞瘤预示着至 HEMM 的时间更短(P=0.005 和 P=0.008)。一线自体移植与至 HEMM 的时间较长相关(P=0.002)。在 HEMM 时,32%的患者骨髓浆细胞增多,20%的患者为非分泌性疾病,43%的患者为轻链疾病。52%的患者有多个 HEMM 部位,主要涉及软组织、皮肤(29%)和胸膜/肺(25%)。首次治疗 HEMM 包括蛋白酶体抑制剂(50%)、免疫调节药物(IMiDs)(39%)、单克隆抗体(10%)和化疗(53%)。总体缓解率(ORR)为 57%。IMiDs 与更高的 ORR 相关(HR 2.2,95%CI 1.02-4.7,P=0.04)。从 HEMM 开始的中位生存期为 6 个月(95%CI 4.8-7.2)。在多变量分析中,未达到≥VGPR 是 OS 较差的唯一显著因素(HR=9.87,95%CI 2.35-39,P=0.001)。总之,HEMM 发生在初始 MM 诊断后的 3 年内,与不良结局相关。IMiDs 可能提供更高的缓解率,达到≥VGPR 预测生存时间更长。