Department of Chemical and Biomolecular Engineering|, New York University, Tandon School of Engineering, 6 MetroTech Center, Brooklyn, NY, 11201, USA.
Appl Biochem Biotechnol. 2020 Apr;190(4):1411-1424. doi: 10.1007/s12010-019-03197-6. Epub 2019 Nov 27.
Aggregation of an amyloid protein, α-synuclein (αS), is a critical step in the neurodegenerative pathway of Parkinson's diseases (PD). Specific detection of amyloid conformers (i.e., monomers, oligomers, and fibrils) produced during αS aggregation is critical in better understanding a molecular basis of PD and developing a diagnostic tool. While various molecular probes are available for detection of αS fibrils, which may serve as a reservoir of toxic αS aggregate forms, these probes suffer from limited conformer-specificity and operational flexibility. In the present study, we explored the potential of non-self-aggregating peptides derived from the highly aggregation-prone KLVFFAE region of an amyloid protein, β-amyloid, as molecular probes for αS aggregates. We show that of the four peptides tested (KLVFWAK, ELVFWAE, and their C-terminal capping variants, all of which were attached with fluorescein isothiocyanate at their respective N-termini), KLVFWAK with C-terminal capping was selectively bound to αS fibrils over monomers and oligomers and readily used for monitoring αS fibrilization. Our analyses suggest that binding of the peptide to αS fibrils is mediated by both electrostatic and hydrophobic interactions. We anticipate that our peptide can readily be optimized for conformer-specificity and operational flexibility. Overall, this study presents the creation of a KLVFFAE-based molecular probe for αS fibrils and demonstrates fine-tuning of its conformer-specificity by terminal mutations and capping.
淀粉样蛋白α-突触核蛋白(αS)的聚集是帕金森病(PD)神经退行性途径中的关键步骤。在更好地理解 PD 的分子基础和开发诊断工具方面,特异性检测αS 聚集过程中产生的淀粉样蛋白构象(即单体、寡聚体和纤维)至关重要。虽然有各种分子探针可用于检测αS 纤维,这些纤维可能是有毒的αS 聚集形式的储库,但这些探针存在构象特异性和操作灵活性有限的问题。在本研究中,我们探索了源自淀粉样蛋白β-淀粉样蛋白的高度聚集倾向的 KLVFFAE 区域的非自身聚集肽作为αS 聚集物的分子探针的潜力。我们表明,在所测试的四个肽(KLVFWAK、ELVFWAE 及其 C 末端加帽变体,它们均在各自的 N 末端连接了异硫氰酸荧光素)中,带 C 末端加帽的 KLVFWAK 选择性地与αS 纤维结合,而不是单体和寡聚体,并且易于用于监测αS 纤维化。我们的分析表明,该肽与αS 纤维的结合是通过静电和疏水相互作用介导的。我们预计,我们的肽可以很容易地针对构象特异性和操作灵活性进行优化。总体而言,这项研究提出了一种基于 KLVFFAE 的用于αS 纤维的分子探针,并通过末端突变和加帽来展示其构象特异性的微调。