Vagelos College of Physicians and Surgeons, Columbia University, New York, NY, USA.
Department of Dermatology, Columbia University Irving Medical Center, New York, NY, USA.
Am J Clin Dermatol. 2020 Jun;21(3):371-381. doi: 10.1007/s40257-019-00500-3.
Conjunctival melanoma is a rare tumor of the conjunctival epithelium with a heterogenous clinical presentation and a propensity for regional and distant metastatic spread. Guidelines for the treatment of local conjunctival melanoma are well-established, but there are no standard efficacious therapies for metastatic disease. Given that conjunctival melanoma is genetically similar to cutaneous melanoma and mucosal melanomas, targeted therapies effective in the treatment of these diseases, such as BRAF inhibitors and KIT inhibitors, may be effective in the treatment of patients with metastatic conjunctival melanoma. Other targeted small-molecule drugs in the drug development pipeline for the treatment of more prevalent melanomas could also be applicable to conjunctival melanoma. Furthermore, systemic immunotherapy treatments that are now a mainstay in the treatment of cutaneous melanoma, such as programmed cell death-1 and cytotoxic T lymphocyte-associated antigen-4 inhibitors, could also stand to benefit patients with metastatic conjunctival melanoma. Limited case reports provide clues about the effectiveness of both targeted small-molecule inhibitors and immunotherapy in patients with advanced local and metastatic conjunctival melanoma and give credence to the argument that conjunctival melanoma patients should be included in major trials studying new therapies in both cutaneous and mucosal melanomas where applicable.
结膜黑色素瘤是一种罕见的结膜上皮肿瘤,具有异质性的临床表现,且易发生区域性和远处转移。局部结膜黑色素瘤的治疗指南已经确立,但对于转移性疾病尚无标准有效的治疗方法。鉴于结膜黑色素瘤在遗传学上与皮肤黑色素瘤和黏膜黑色素瘤相似,针对这些疾病有效的靶向治疗药物,如 BRAF 抑制剂和 KIT 抑制剂,可能对转移性结膜黑色素瘤患者有效。治疗更常见黑色素瘤的药物研发管道中的其他靶向小分子药物也可能适用于结膜黑色素瘤。此外,目前已成为皮肤黑色素瘤治疗主要手段的全身性免疫治疗药物,如程序性细胞死亡蛋白-1 和细胞毒性 T 淋巴细胞相关抗原-4 抑制剂,也可能使转移性结膜黑色素瘤患者受益。有限的病例报告为晚期局部和转移性结膜黑色素瘤患者的靶向小分子抑制剂和免疫治疗的有效性提供了线索,并使人们相信,应将结膜黑色素瘤患者纳入研究皮肤和黏膜黑色素瘤新疗法的主要临床试验中,只要适用。