Unidad de Transferencia Genética, Instituto de Oncología "Ángel H. Roffo", Universidad de Buenos Aires, Buenos Aires, Argentina.
Gene Ther. 2021 Feb;28(1-2):38-55. doi: 10.1038/s41434-020-0136-x. Epub 2020 Mar 3.
In the context of comparative oncology, melanoma cells derived from companion animal tumors are good models for optimizing and predicting their in vivo response to therapeutic strategies. Here, we report that human, canine, and feline melanoma cells driven to death by bleomycin, interferon-β gene, or herpes simplex virus thymidine kinase/ganciclovir suicide gene (SG) treatment significantly increased their internal granularity. This fact correlated with the release of a heterogeneous collection of nano- and micro-sized granules as revealed by transmission electron microscopy. While killing lipofected cells, the expressed transgenes and their derived products were incorporated into these granules that were isolated by differential centrifugation. These particulate factors (PFs) were able to transfer, in a dose- and time-dependent manner, appreciable levels of therapeutic genes, related proteins, and drugs. Thus, when recipient cells of SG-carrying PFs were exposed to ganciclovir, this prodrug was efficiently activated, eliminating them. These PFs kept the functionality of their cargo, even after being subjected to adverse conditions, such as the presence of DNase, freezing, or heating. Since our in vitro system did not include any of the immune mechanisms that could provide additional antitumor activity, the chemo-gene treatments amplified by these delivery bags of therapeutic agents offer a great clinical potential.
在比较肿瘤学领域,源自伴侣动物肿瘤的黑色素瘤细胞是优化和预测其对治疗策略的体内反应的良好模型。在这里,我们报告说,通过博来霉素、干扰素-β基因或单纯疱疹病毒胸苷激酶/更昔洛韦自杀基因 (SG) 治疗而死亡的人、犬和猫黑色素瘤细胞,其内部颗粒显著增加。这一事实与透射电子显微镜显示的异质纳米和微颗粒混合物的释放有关。在杀死转染细胞的同时,表达的转基因及其衍生产物被整合到通过差速离心分离的这些颗粒中。这些颗粒因子 (PFs) 能够以剂量和时间依赖的方式转移相当水平的治疗基因、相关蛋白和药物。因此,当携带 SG 的 PFs 的受体细胞暴露于更昔洛韦时,这种前药被有效激活并将其杀死。即使在经受 DNA 酶、冷冻或加热等不利条件后,这些 PFs 仍能保持其货物的功能。由于我们的体外系统不包括任何可能提供额外抗肿瘤活性的免疫机制,因此这些治疗药物的输送袋增强的化学-基因治疗提供了巨大的临床潜力。