Ph.D. Program in Biotechnology Research and Development, Taipei Medical University, Taipei, Taiwan.
School of Pharmacy, Taipei Medical University, Taipei, Taiwan.
Eur J Med Chem. 2020 Apr 15;192:112193. doi: 10.1016/j.ejmech.2020.112193. Epub 2020 Feb 29.
Multitarget agents simultaneously trigger molecules in functionally complementary pathways, and are therefore considered to have potential in effectively treating Alzheimer's disease (AD), which has a complex pathogenetic mechanism. In this study, the HDAC inhibitor core is incorporated into the acetylcholine esterase (ACE) inhibitor acridine-derived moiety and resulted in compounds that exhibited higher class IIa HDAC (4, 5, 7, and 9)- and class IIb HDAC6-inhibiting activity when compared to the pan-HDAC inhibitor SAHA in clinical practice. One of these compounds, 11b, displayed greater selectivity toward HDAC6 than other isoform enzymes. In contrast, the activity of compound 6a was selective toward class IIa HDAC and HDAC6. These two compounds exhibited strong activity against Aβ-aggregation as well as significantly disrupted Aβ-oligomer. Additionally, 11b and 6a strongly inhibited AChE. These experimental findings demonstrate that compounds 11b and 6a are HDAC-Aβ-aggregation-AChE inhibitors. Notably, they can enhance neurite outgrowth, but with no significant neurotoxicity. Further biological evaluation revealed the various cellular effects of multitarget compounds 11b and 6a, which have the potential to treat AD.
多靶点药物同时作用于功能互补的分子途径,因此被认为具有有效治疗阿尔茨海默病(AD)的潜力,AD 具有复杂的发病机制。在这项研究中,将 HDAC 抑制剂核心整合到乙酰胆碱酯酶(ACE)抑制剂吖啶衍生部分中,得到的化合物与临床上使用的泛 HDAC 抑制剂 SAHA 相比,对 IIa 类(4、5、7 和 9)和 IIb 类 HDAC6 的抑制活性更高。这些化合物中的一种,11b,对 HDAC6 的选择性高于其他同工酶。相比之下,化合物 6a 的活性对 IIa 类 HDAC 和 HDAC6 具有选择性。这两种化合物对 Aβ 聚集具有很强的活性,并且可以显著破坏 Aβ 寡聚物。此外,11b 和 6a 强烈抑制 AChE。这些实验结果表明,化合物 11b 和 6a 是 HDAC-Aβ 聚集-AChE 抑制剂。值得注意的是,它们可以促进神经突生长,但没有明显的神经毒性。进一步的生物学评估揭示了多靶点化合物 11b 和 6a 的各种细胞作用,它们具有治疗 AD 的潜力。