Suppr超能文献

孤立性肾钙质沉着症归因于肾外髓质钾通道的复合杂合突变。

Isolated nephrocalcinosis due to compound heterozygous mutations in renal outer medullary potassium channel.

机构信息

Division of Nephrology, Department of Pediatrics, All India Institute of Medical Sciences, Ansari Nagar, New Delhi, 110029, India.

出版信息

CEN Case Rep. 2020 Aug;9(3):232-236. doi: 10.1007/s13730-020-00464-y. Epub 2020 Mar 17.

Abstract

Identification of a monogenic etiology is possible in a proportion of patients with childhood-onset nephrolithiasis or nephrocalcinosis. Bartter syndrome (BS), a hereditary tubulopathy characterized by polyuria, hypokalemic alkalosis and growth retardation that rarely presents with isolated nephrocalcinosis. Patients with defect in renal outer medullary potassium channel, encoded by the KCNJ1 gene causing BS type 2, typically present during the neonatal period. We describe a 14-year-old girl with mild late-onset BS type 2 with reported pathogenic compound heterozygous variations in exon 2 of KCNJ1 (c.146G > A and c.657C > G). This patient presented with isolated medullary nephrocalcinosis due to hypercalciuria; absence of hypokalemia and metabolic alkalosis was unique. This case highlights the importance of screening the KCNJ1 gene in patients with hypercalciuria and nephrocalcinosis, even in older children.

摘要

在一部分儿童期起病的肾结石或肾钙质沉着症患者中,可能存在单基因病因。巴特综合征(Bartter syndrome,BS)是一种遗传性肾小管病,以多尿、低钾性碱中毒和生长迟缓为特征,很少表现为孤立性肾钙质沉着症。由 KCNJ1 基因编码的肾脏外髓质钾通道缺陷导致 BS 型 2,通常在新生儿期出现。我们描述了一名 14 岁女孩患有轻度晚发型 BS 型 2,该患者在 KCNJ1 基因的外显子 2中存在报道的致病性复合杂合变异(c.146G>A 和 c.657C>G)。该患者由于高钙尿症而出现孤立性髓质肾钙质沉着症;低钾血症和代谢性碱中毒的缺失是独特的。该病例强调了在高钙尿症和肾钙质沉着症患者中筛查 KCNJ1 基因的重要性,即使是在年龄较大的儿童中。

相似文献

引用本文的文献

本文引用的文献

1
Bartter and Gitelman syndromes: Questions of class.巴特综合征和吉特曼综合征:分类问题。
Pediatr Nephrol. 2020 Oct;35(10):1815-1824. doi: 10.1007/s00467-019-04371-y. Epub 2019 Oct 29.
5
Late-onset Bartter syndrome type II.迟发性II型巴特综合征
Clin Kidney J. 2017 Oct;10(5):594-599. doi: 10.1093/ckj/sfx033. Epub 2017 May 8.
7
Clinical and Genetic Spectrum of Bartter Syndrome Type 3.3型巴特综合征的临床和遗传谱系
J Am Soc Nephrol. 2017 Aug;28(8):2540-2552. doi: 10.1681/ASN.2016101057. Epub 2017 Apr 5.
8
Bartter's and Gitelman's syndrome.巴特综合征和吉特曼综合征。
Curr Opin Pediatr. 2017 Apr;29(2):179-186. doi: 10.1097/MOP.0000000000000447.
10
Accentuated hyperparathyroidism in type II Bartter syndrome.II型巴特综合征中甲状旁腺功能亢进加重
Pediatr Nephrol. 2016 Jul;31(7):1085-90. doi: 10.1007/s00467-016-3337-1. Epub 2016 Feb 8.

文献检索

告别复杂PubMed语法,用中文像聊天一样搜索,搜遍4000万医学文献。AI智能推荐,让科研检索更轻松。

立即免费搜索

文件翻译

保留排版,准确专业,支持PDF/Word/PPT等文件格式,支持 12+语言互译。

免费翻译文档

深度研究

AI帮你快速写综述,25分钟生成高质量综述,智能提取关键信息,辅助科研写作。

立即免费体验