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本文引用的文献

1
Histone-induced thrombotic thrombocytopenic purpura in zebrafish depends on von Willebrand factor.组蛋白诱导的血栓性血小板减少性紫癜在斑马鱼中依赖于血管性血友病因子。
Haematologica. 2020 Apr;105(4):1107-1119. doi: 10.3324/haematol.2019.237396. Epub 2019 Nov 21.
2
The International Hereditary Thrombotic Thrombocytopenic Purpura Registry: key findings at enrollment until 2017.国际遗传性血栓性血小板减少性紫癜登记处:2017 年前登记时的主要发现。
Haematologica. 2019 Oct;104(10):2107-2115. doi: 10.3324/haematol.2019.216796. Epub 2019 Feb 21.
3
Thrombotic thrombocytopenic purpura: Toward targeted therapy and precision medicine.血栓性血小板减少性紫癜:迈向靶向治疗与精准医学
Res Pract Thromb Haemost. 2018 Nov 16;3(1):26-37. doi: 10.1002/rth2.12160. eCollection 2019 Jan.
4
Caplacizumab Treatment for Acquired Thrombotic Thrombocytopenic Purpura.卡普拉珠单抗治疗获得性血栓性血小板减少性紫癜。
N Engl J Med. 2019 Jan 24;380(4):335-346. doi: 10.1056/NEJMoa1806311. Epub 2019 Jan 9.
5
ADAMTS13 Gene Mutations Influence ADAMTS13 Conformation and Disease Age-Onset in the French Cohort of Upshaw-Schulman Syndrome.ADAMTS13 基因突变影响法国 Upshaw-Schulman 综合征队列中 ADAMTS13 构象和发病年龄。
Thromb Haemost. 2018 Nov;118(11):1902-1917. doi: 10.1055/s-0038-1673686. Epub 2018 Oct 12.
6
Clinical factors and biomarkers predict outcome in patients with immune-mediated thrombotic thrombocytopenic purpura.临床因素和生物标志物可预测免疫性血栓性血小板减少性紫癜患者的结局。
Haematologica. 2019 Jan;104(1):166-175. doi: 10.3324/haematol.2018.198275. Epub 2018 Aug 31.
7
Recombinant ADAMTS-13: first-in-human pharmacokinetics and safety in congenital thrombotic thrombocytopenic purpura.重组ADAMTS-13:先天性血栓性血小板减少性紫癜的首次人体药代动力学和安全性研究
Blood. 2017 Nov 9;130(19):2055-2063. doi: 10.1182/blood-2017-06-788026. Epub 2017 Sep 14.
8
Presenting ADAMTS13 antibody and antigen levels predict prognosis in immune-mediated thrombotic thrombocytopenic purpura.ADAMTS13 抗体和抗原水平与免疫性血栓性血小板减少性紫癜的预后相关。
Blood. 2017 Jul 27;130(4):466-471. doi: 10.1182/blood-2016-12-758656. Epub 2017 Jun 2.
9
Thrombotic thrombocytopenic purpura.血栓性血小板减少性紫癜。
Nat Rev Dis Primers. 2017 Apr 6;3:17020. doi: 10.1038/nrdp.2017.20.
10
-acetylcysteine in preclinical mouse and baboon models of thrombotic thrombocytopenic purpura.在血栓性血小板减少性紫癜的临床前小鼠和狒狒模型中使用乙酰半胱氨酸。
Blood. 2017 Feb 23;129(8):1030-1038. doi: 10.1182/blood-2016-09-738856. Epub 2016 Dec 23.

Animal models of thrombotic thrombocytopenic purpura: the tales from zebrafish.

作者信息

Coppo Paul, Lämmle Bernhard

机构信息

Service d'Hématologie, Centre de Référence des Microangiopathies Thrombotiques, AP-HP.6, Paris, France

Department of Hematology and Central Hematology Laboratory, Inselspital, Bern University Hospital, University of Bern, Bern Switzerland

出版信息

Haematologica. 2020 Apr;105(4):861-863. doi: 10.3324/haematol.2019.245043.

DOI:10.3324/haematol.2019.245043
PMID:32238467
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC7109746/
Abstract
摘要