Institute of Medical Genetics, Tokyo Women's Medical University, 8-1 Kawada-cho, Shinjuku-ward, Tokyo, 162-8666, Japan.
Department of Pediatrics, St. Marianna University School of Medicine, Kawasaki, Japan.
Hum Genet. 2020 Dec;139(12):1555-1563. doi: 10.1007/s00439-020-02196-6. Epub 2020 Jun 13.
The chromosomal region critical in Down syndrome has long been analyzed through genotype-phenotype correlation studies using data from many patients with partial trisomy 21. Owing to that, a relatively small region of human chromosome 21 (35.9 ~ 38.0 Mb) has been considered as Down syndrome critical region (DSCR). In this study, microarray-based comparative genomic hybridization analysis identified complex rearrangements of chromosome 21 in a patient manifesting clinical features partially overlapped with that of Down syndrome. Although the patient did not show up-slanting palpebral fissures and single transverse palmar creases, other symptoms were consistent with Down syndrome. Rearrangements were analyzed by whole-genome sequencing using Nanopore long-read sequencing. The analysis revealed that chromosome 21 was fragmented into seven segments and reassembled by six connected points. Among 12 breakpoints, 5 are located within the short region and overlapped with repeated segments. The rearrangement resulted in a maximum gain of five copies, but no region showed loss of genomic copy numbers. Breakpoint-junctions showed no homologous region. Based on these findings, chromoanasynthesis was considered as the mechanism. Although the distal 21q22.13 region was not included in the aberrant regions, some of the genes located on the duplicated regions, SOD1, SON, ITSN1, RCAN1, and RUNX1, were considered as possible candidate genes for clinical features of the patient. We discussed the critical region for Down syndrome, with the literature review.
唐氏综合征的关键染色体区域长期以来一直通过使用来自许多部分三体 21 患者的数据进行基因型 - 表型相关性研究进行分析。由于此,人类染色体 21 上的一个相对较小的区域(35.9 至 38.0 Mb)被认为是唐氏综合征关键区域(DSCR)。在这项研究中,基于微阵列的比较基因组杂交分析鉴定了表现出与唐氏综合征部分重叠的临床特征的患者的 21 号染色体复杂重排。尽管患者没有表现出斜向上眼睑裂缝和单一横向手掌折痕,但其他症状与唐氏综合征一致。使用 Nanopore 长读测序对全基因组测序进行了重排分析。分析表明,21 号染色体被分成七个片段,并通过六个连接点重新组装。在 12 个断点中,有 5 个位于短区域内并与重复片段重叠。重排导致最大增益为五个拷贝,但没有区域显示基因组拷贝数的损失。断点连接处没有同源区域。基于这些发现,考虑了染色体重组作为机制。尽管异常区域不包括远端 21q22.13 区域,但位于重复区域上的一些基因,如 SOD1、SON、ITSN1、RCAN1 和 RUNX1,被认为是患者临床特征的可能候选基因。我们讨论了唐氏综合征的关键区域,并进行了文献回顾。