Department of Cell Biology and Biochemistry, Texas Tech University Health Sciences Center, Lubbock, TX 79430.
Department of Chemistry and Biochemistry, Texas Tech University, Lubbock, TX 79409.
Proc Natl Acad Sci U S A. 2020 Jul 14;117(28):16363-16372. doi: 10.1073/pnas.2006887117. Epub 2020 Jun 29.
The epididymal lumen contains a complex cystatin-rich nonpathological amyloid matrix with putative roles in sperm maturation and sperm protection. Given our growing understanding for the biological function of this and other functional amyloids, the problem still remains: how functional amyloids assemble including their initial transition to early oligomeric forms. To examine this, we developed a protocol for the purification of nondenatured mouse CRES, a component of the epididymal amyloid matrix, allowing us to examine its assembly to amyloid under conditions that may mimic those in vivo. Herein we use X-ray crystallography, solution-state NMR, and solid-state NMR to follow at the atomic level the assembly of the CRES amyloidogenic precursor as it progressed from monomeric folded protein to an advanced amyloid. We show the CRES monomer has a typical cystatin fold that assembles into highly branched amyloid matrices, comparable to those in vivo, by forming β-sheet assemblies that our data suggest occur via two distinct mechanisms: a unique conformational switch of a highly flexible disulfide-anchored loop to a rigid β-strand and by traditional cystatin domain swapping. Our results provide key insight into our understanding of functional amyloid assembly by revealing the earliest structural transitions from monomer to oligomer and by showing that some functional amyloid structures may be built by multiple and distinctive assembly mechanisms.
附睾管腔中含有一种复杂的富含半胱氨酸蛋白酶抑制剂的无病理性淀粉样基质,其可能在精子成熟和精子保护中发挥作用。鉴于我们对这种和其他功能性淀粉样蛋白的生物学功能的理解不断加深,问题仍然存在:功能性淀粉样蛋白是如何组装的,包括它们向早期寡聚体形式的初始转变。为了研究这个问题,我们开发了一种纯化未变性的小鼠 CRES 的方案,CRES 是附睾淀粉样基质的一个组成部分,使我们能够在可能模拟体内条件的情况下研究其淀粉样组装。在这里,我们使用 X 射线晶体学、溶液状态 NMR 和固态 NMR 从原子水平上跟踪 CRES 淀粉样前体的组装,该前体从单体折叠蛋白进展为高级淀粉样蛋白。我们表明,CRES 单体具有典型的半胱氨酸蛋白酶抑制剂折叠,通过形成β-折叠组装,组装成高度分支的淀粉样基质,与体内的基质相当,我们的数据表明,这些β-折叠组装通过两种不同的机制发生:高度灵活的二硫键锚定环的独特构象转换为刚性β-链,以及通过传统的半胱氨酸蛋白酶抑制剂结构域交换。我们的结果通过揭示单体到寡聚体的最早结构转变,并通过显示一些功能性淀粉样蛋白结构可能由多种独特的组装机制构建,为我们对功能性淀粉样蛋白组装的理解提供了关键的见解。