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Gene therapy to cure haemophilia: Is robust scientific inquiry the missing factor?

作者信息

Pierce Glenn F, Kaczmarek Radoslaw, Noone Declan, O'Mahony Brian, Page David, Skinner Mark W

机构信息

World Federation of Hemophilia, Montreal, QC, Canada.

Polish Hemophilia Society, Warsaw, Poland.

出版信息

Haemophilia. 2020 Nov;26(6):931-933. doi: 10.1111/hae.14131. Epub 2020 Sep 10.

DOI:10.1111/hae.14131

PMID:32909632

Abstract

摘要

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相似文献

Gene therapy to cure haemophilia: Is robust scientific inquiry the missing factor?

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Expert Opin Biol Ther. 2004 Jun;4(6):763-6. doi: 10.1517/14712598.4.6.763.

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Haemophilia. 1998 Jul;4(4):380-8. doi: 10.1046/j.1365-2516.1998.440380.x.

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