Department of Genetics, University of Groningen, University Medical Center Groningen, Groningen, The Netherlands.
Department of Rehabilitation Medicine, University of Groningen, University Medical Center Groningen, Groningen, The Netherlands.
Am J Med Genet A. 2020 Dec;182(12):2909-2918. doi: 10.1002/ajmg.a.61875. Epub 2020 Sep 21.
Limb reduction defects (LRDs) that affect multiple limbs are considered to be more often heritable, but only few studies have substantiated this. We aimed to investigate if an etiological diagnosis (genetic disorder or clinically recognizable disorder) is more likely to be made when multiple limbs are affected compared to when only one limb is affected. We used data from EUROCAT Northern Netherlands and included 391 fetuses and children with LRDs born in 1981-2017. Cases were classified as having a transverse, longitudinal (preaxial/postaxial/central/mixed), intercalary, or complex LRD of one or more limbs and as having an isolated LRD or multiple congenital anomalies (MCA). We calculated the probability of obtaining an etiological diagnosis in cases with multiple affected limbs versus one affected limb using relative risk (RR) scores and Fisher's exact test. We showed that an etiological diagnosis was made three times more often when an LRD occurred in multiple limbs compared to when it occurred in one limb (RR 2.9, 95% CI 2.2-3.8, p < 0.001). No genetic disorders were found in isolated cases with only one affected limb, whereas a genetic disorder was identified in 16% of MCA cases with one affected limb. A clinically recognizable disorder was found in 47% of MCA cases with one affected limb. Genetic counseling rates were similar. We conclude that reduction defects of multiple limbs are indeed more often heritable. Genetic testing seems less useful in isolated cases with one affected limb, but is warranted in MCA cases with one affected limb.
肢体减少缺陷(LRD)影响多个肢体被认为更常具有遗传性,但仅有少数研究证实了这一点。我们旨在调查当多个肢体受到影响时,是否比只有一个肢体受到影响时更有可能做出病因诊断(遗传障碍或临床可识别的障碍)。我们使用了 EUROCAT 荷兰北部的数据,纳入了 1981 年至 2017 年间出生的 391 名患有 LRD 的胎儿和儿童。病例被分为具有横向、纵向(前轴/后轴/中央/混合)、中间或复杂的一个或多个肢体 LRD,以及具有孤立性 LRD 或多发性先天性异常(MCA)。我们使用相对风险(RR)评分和 Fisher 确切检验计算了多个受累肢体与一个受累肢体的病例获得病因诊断的概率。我们表明,与一个肢体受累相比,多个肢体受累的 LRD 发生时病因诊断的可能性高三倍(RR 2.9,95%CI 2.2-3.8,p<0.001)。在仅有一个受累肢体的孤立性病例中未发现遗传障碍,而在仅有一个受累肢体的 MCA 病例中,有 16%被诊断为遗传障碍。在仅有一个受累肢体的 MCA 病例中,有 47%被诊断为临床可识别的障碍。遗传咨询率相似。我们得出结论,多个肢体的减少缺陷确实更常具有遗传性。在仅有一个受累肢体的孤立性病例中,遗传检测的作用不大,但在仅有一个受累肢体的 MCA 病例中,遗传检测是合理的。