AlFaris Haya S, Elhissi Ghasan, Chedrawi Aziza, Al-Muhaizea Mohammad A
College of Medicine, Alfaisal University, Riyadh, Saudi Arabia.
Division of Pediatric Neurology, Department of Neurosciences, King Faisal Specialist Hospital and Research Centre, Riyadh, Saudi Arabia.
Int J Pediatr Adolesc Med. 2021 Mar;8(1):52-54. doi: 10.1016/j.ijpam.2020.01.003. Epub 2020 Jan 17.
Recessive congenital methemoglobinemia (RCM) is a rare neurological disorder caused by a deficiency in NADH-CYB5R. RCM has two main types I&II, with cyanosis being the hallmark feature in both. Type-I is a mild form, with cyanosis being the only feature. While type-II is the severe form with prominent neurological symptoms including, dystonia and spasticity. However, the cyanosis is subtle and difficult to appreciate. The cyanosis in RCM is treated with ascorbic-acid or methylene-blue. However, those treatments will not alter the neurological complication. In this paper, we report two cases of RCM type-II in Saudi siblings. They presented with cyanosis at birth; a CO-oximetry was done showing a high level of methemoglobin and a trail of methylene blue was used. The siblings were followed up and showed signs of developmental delay, hypotonia, exaggerated reflex, and seizure. A genetic analysis was requested, which showed missense mutation (c.274 C > T), leading to amino acid substitution; p. Arg92Trp.
隐性先天性高铁血红蛋白血症(RCM)是一种由NADH-细胞色素b5还原酶缺乏引起的罕见神经系统疾病。RCM主要有I型和II型两种类型,二者的标志性特征均为发绀。I型为轻型,发绀是唯一特征。而II型为重型,伴有明显的神经症状,包括肌张力障碍和痉挛。然而,其发绀症状不明显,难以察觉。RCM的发绀采用抗坏血酸或亚甲蓝治疗。不过,这些治疗方法不会改变神经并发症。在本文中,我们报告了沙特一对兄弟姐妹患II型RCM的病例。他们出生时即出现发绀;进行了一氧化碳血氧定量分析,结果显示高铁血红蛋白水平升高,并使用了亚甲蓝进行治疗。对这对兄弟姐妹进行了随访,发现有发育迟缓、肌张力减退、反射亢进和癫痫发作的迹象。进行了基因分析,结果显示存在错义突变(c.274 C>T),导致氨基酸替换;p.Arg92Trp。