Division of Medical Oncology and Hematology, Princess Margaret Cancer Centre, Toronto, ON, Canada.
Bone Marrow Transplant. 2021 Oct;56(10):2400-2409. doi: 10.1038/s41409-021-01327-5. Epub 2021 May 13.
This study compared the quality-adjusted effectiveness and costs of three treatment options for transplant-eligible patients with early progression (POD24) of follicular lymphoma. A Markov decision-analytic model using a 20-year time horizon was used to compare allogeneic stem cell transplant (alloSCT), autologous stem cell transplant (ASCT), and chemo-immunotherapy (O-CHOP). For second relapse/refractory disease, novel therapy use was modeled, including lenalidomide and rituximab/obinutuzumab, and PI3K inhibitors (PI3Ki). Costs were considered from a Canadian public health payer's perspective. Probabilistic analyses (10,000 simulations) demonstrated that at a willingness-to-pay threshold of $50,000, ASCT was most cost effective 60% of the time. ASCT resulted in more life years (10.2 vs. alloSCT 9.9 vs. O-CHOP 10.0) and quality-adjusted life years (7.5 vs. alloSCT 6.6 vs. O-CHOP 7.4), with the lowest direct costs ($190,128 CAD). In sensitivity analyses, the model was robust to key variables, including differing probabilities of progression, non-relapse mortality, graft-versus-host-disease (GVHD), costs of treating GVHD, costs of PI3Ki, and probability of secondary malignancy from ASCT. However, if patients were older than 65 years or their life expectancy was less than 10 years, chemo-immunotherapy was the preferred strategy. When considering cost, effectiveness, and toxicities, the preferred treatment strategy for most patients with POD24 follicular lymphoma is ASCT.
这项研究比较了三种治疗方案在滤泡性淋巴瘤早期进展(POD24)患者中的疗效和成本。采用 20 年时间范围的马尔可夫决策分析模型,比较了异基因造血干细胞移植(alloSCT)、自体造血干细胞移植(ASCT)和化疗免疫治疗(O-CHOP)。对于第二次复发/难治性疾病,模型中考虑了新的治疗方法,包括来那度胺和利妥昔单抗/奥滨尤妥珠单抗以及 PI3K 抑制剂(PI3Ki)。从加拿大公共卫生支付者的角度考虑了成本。概率分析(10000 次模拟)表明,在愿意支付 5 万美元的阈值下,ASCT 有 60%的时间最具成本效益。ASCT 导致更多的生命年(10.2 年比 alloSCT 9.9 年比 O-CHOP 10.0 年)和质量调整生命年(7.5 年比 alloSCT 6.6 年比 O-CHOP 7.4 年),直接成本最低(190128 加元)。在敏感性分析中,该模型对关键变量具有稳健性,包括不同的进展概率、非复发死亡率、移植物抗宿主病(GVHD)、治疗 GVHD 的成本、PI3Ki 的成本以及 ASCT 后继发性恶性肿瘤的概率。然而,如果患者年龄大于 65 岁或预期寿命小于 10 年,则化疗免疫治疗是首选策略。考虑成本、效果和毒性,对于大多数 POD24 滤泡性淋巴瘤患者,首选的治疗策略是 ASCT。