School of Pharmacy & Biomedical Sciences, University of Portsmouth, St Michael's Building, White Swan Road, Portsmouth, PO12DT, UK.
Leicester School of Pharmacy, De Montfort University, Leicester, LE1 9BH, UK.
Cell Mol Neurobiol. 2022 Oct;42(7):2357-2377. doi: 10.1007/s10571-021-01110-6. Epub 2021 Jun 8.
Duchenne muscular dystrophy (DMD) patients, having mutations of the DMD gene, present with a range of neuropsychiatric disorders, in addition to the quintessential muscle pathology. The neurobiological basis remains poorly understood because the contributions of different DMD gene products (dystrophins) to the different neural networks underlying such symptoms are yet to be fully characterised. While full-length dystrophin clusters in inhibitory synapses, with inhibitory neurotransmitter receptors, the precise subcellular expression of truncated DMD gene products with excitatory synapses remains unresolved. Furthermore, inflammation, involving P2X purinoceptor 7 (P2RX7) accompanies DMD muscle pathology, yet any association with brain dystrophins is yet to be established. The aim of this study was to investigate the comparative expression of different dystrophins, alongside ionotropic glutamate receptors and P2RX7s, within the cerebellar circuitry known to express different dystrophin isoforms. Immunoreactivity for truncated DMD gene products was targeted to Purkinje cell (PC) distal dendrites adjacent to, or overlapping with, signal for GluA1, GluA4, GluN2A, and GluD2 receptor subunits. P2X7R immunoreactivity was located in Bergmann glia profiles adjacent to PC-dystrophin immunoreactivity. Ablation of all DMD gene products coincided with decreased mRNA expression for Gria2, Gria3, and Grin2a and increased GluD2 immunoreactivity. Finally, dystrophin-null mice showed decreased brain mRNA expression of P2rx7 and several inflammatory mediators. The data suggest that PCs target different dystrophin isoforms to molecularly and functionally distinct populations of synapses. In contrast to muscle, dystrophinopathy in brain leads to the dampening of the local immune system.
杜氏肌营养不良症(DMD)患者由于 DMD 基因突变,除了典型的肌肉病理外,还表现出一系列神经精神障碍。神经生物学基础仍知之甚少,因为不同 DMD 基因突变产物(肌营养不良蛋白)对潜在此类症状的不同神经网络的贡献尚未完全确定。虽然全长肌营养不良蛋白聚集在抑制性突触中,与抑制性神经递质受体结合,但截断的 DMD 基因突变产物在兴奋性突触中的精确亚细胞表达仍未解决。此外,涉及 P2X 嘌呤能受体 7(P2RX7)的炎症伴随着 DMD 肌肉病理学,但与大脑肌营养不良蛋白的任何关联尚未建立。本研究旨在研究不同肌营养不良蛋白,以及离子型谷氨酸受体和 P2RX7,在已知表达不同肌营养不良蛋白同工型的小脑回路中的比较表达。针对截断的 DMD 基因突变产物的免疫反应性靶向 Purkinje 细胞(PC)远端树突,这些树突紧邻或重叠 GluA1、GluA4、GluN2A 和 GluD2 受体亚基的信号。P2X7R 免疫反应位于与 PC-肌营养不良蛋白免疫反应相邻的 Bergmann 神经胶质突起中。所有 DMD 基因突变产物的缺失与 Gria2、Gria3 和 Grin2a 的 mRNA 表达减少以及 GluD2 免疫反应性增加同时发生。最后,肌营养不良蛋白缺失小鼠表现出大脑中 P2rx7 和几种炎症介质的 mRNA 表达减少。数据表明,PC 将不同的肌营养不良蛋白同工型靶向到分子和功能上不同的突触群。与肌肉不同,大脑中的肌营养不良蛋白病导致局部免疫系统的抑制。