Suppr超能文献

在有删失随访的临床试验中曲线下面积的组间比较:在HIV治疗性疫苗中的应用

Between-group comparison of area under the curve in clinical trials with censored follow-up: Application to HIV therapeutic vaccines.

作者信息

Alexandre Marie, Prague Mélanie, Thiébaut Rodolphe

机构信息

University of Bordeaux, Inria Bordeaux Sud-Ouest, Inserm, Bordeaux Population Health Research Center, SISTM Team, France.

Data Science Division, Vaccine Research Institute (VRI), Créteil, France.

出版信息

Stat Methods Med Res. 2021 Sep;30(9):2130-2147. doi: 10.1177/09622802211023963. Epub 2021 Jul 4.

Abstract

In clinical trials, longitudinal data are commonly analyzed and compared between groups using a single summary statistic such as area under the outcome versus time curve (AUC). However, incomplete data, arising from censoring due to a limit of detection or missing data, can bias these analyses. In this article, we present a statistical test based on splines-based mixed-model accounting for both the censoring and missingness mechanisms in the AUC estimation. Inferential properties of the proposed method were evaluated and compared to ad hoc approaches and to a non-parametric method through a simulation study based on two-armed trial where trajectories and the proportion of missing data were varied. Simulation results highlight that our approach has significant advantages over the other methods. A real working example from two HIV therapeutic vaccine trials is presented to illustrate the applicability of our approach.

摘要

在临床试验中,纵向数据通常通过单个汇总统计量(如结局随时间曲线下面积(AUC))在组间进行分析和比较。然而,由于检测限导致的删失或数据缺失而产生的不完整数据,可能会使这些分析产生偏差。在本文中,我们提出了一种基于样条的混合模型的统计检验方法,该方法在AUC估计中同时考虑了删失和缺失机制。通过基于双臂试验的模拟研究,对所提方法的推断特性进行了评估,并与临时方法和非参数方法进行了比较,其中轨迹和缺失数据的比例有所不同。模拟结果表明,我们的方法比其他方法具有显著优势。还给出了两个HIV治疗性疫苗试验的实际工作示例,以说明我们方法的适用性。

文献检索

告别复杂PubMed语法,用中文像聊天一样搜索,搜遍4000万医学文献。AI智能推荐,让科研检索更轻松。

立即免费搜索

文件翻译

保留排版,准确专业,支持PDF/Word/PPT等文件格式,支持 12+语言互译。

免费翻译文档

深度研究

AI帮你快速写综述,25分钟生成高质量综述,智能提取关键信息,辅助科研写作。

立即免费体验