Duchenne 型肌营养不良症和脊髓性肌萎缩症的临床结局评估：过去、现在和未来。
Clinical outcome assessments in Duchenne muscular dystrophy and spinal muscular atrophy: past, present and future.
机构信息
Department of Physical Therapy, University of Texas Southwestern Medical Center, 6011 Harry Hines Blvd, Dallas, TX, United States.
Department of Pediatrics and Neurology, University of Texas Southwestern Medical Center, 5323 Harry Hines Blvd, Dallas, TX, United States.
出版信息
Neuromuscul Disord. 2021 Oct;31(10):1028-1037. doi: 10.1016/j.nmd.2021.07.015. Epub 2021 Jul 27.
Scores and scales used in pediatric motor development for neuromuscular disorders have evolved greatly since the beginning of their development. In this review we provide a brief history of scales used in pediatric patients with neuromuscular disorders and an update regarding the advancement of the scales commonly used in patients with spinal muscular atrophy and Duchenne muscular dystrophy. We focus on the collaborative effort that has led to the development of outcomes and speak to the possible future of Clinical Outcome Assessments.
自发展之初以来，用于神经肌肉疾病儿童运动发育的评分和量表已经有了很大的发展。在这篇综述中，我们提供了神经肌肉疾病儿科患者使用的量表的简要历史，并更新了常用于脊髓性肌萎缩症和杜氏肌营养不良症患者的量表的进展情况。我们专注于导致结局发展的协作努力，并探讨临床结局评估的可能未来。
Zotero 插件