Division of Rheumatology, Department of Internal Medicine, University of Michigan, Ann Arbor, MI, USA.
University of Michigan Scleroderma Program, Michigan Medicine, Ann Arbor, MI, USA.
Nat Rev Rheumatol. 2021 Oct;17(10):596-607. doi: 10.1038/s41584-021-00683-2. Epub 2021 Sep 3.
Systemic sclerosis (SSc) is a prototypical inflammatory fibrotic disease involving inflammation, vascular abnormalities and fibrosis that primarily affect the skin and lungs. The aetiology of SSc is unknown and its pathogenesis is only partially understood. Of all the rheumatic diseases, SSc carries the highest all-cause mortality rate and represents an unmet medical need. A growing body of evidence implicates epigenetic aberrations in this intractable disease, including specific modifications affecting the three main cell types involved in SSc pathogenesis: immune cells, endothelial cells and fibroblasts. In this Review, we discuss the latest insights into the role of DNA methylation, histone modifications and non-coding RNAs in SSc and how these epigenetic alterations affect disease features. In particular, histone modifications have a role in the regulation of gene expression pertinent to activation of fibroblasts to myofibroblasts, governing their fate. DNA methyltransferases are crucial in disease pathogenesis by mediating methylation of DNA in specific promoters, regulating expression of specific pathways. We discuss targeting of these enzymes for therapeutic gain. Innovative epigenetic therapy could be targeted to treat the disease in a precision epigenetics approach.
系统性硬化症(SSc)是一种典型的炎症性纤维化疾病,涉及炎症、血管异常和纤维化,主要影响皮肤和肺部。SSc 的病因不明,其发病机制也只是部分了解。在所有风湿性疾病中,SSc 的全因死亡率最高,代表着未满足的医疗需求。越来越多的证据表明,表观遗传异常与这种难治性疾病有关,包括影响 SSc 发病机制中三种主要细胞类型(免疫细胞、内皮细胞和成纤维细胞)的特定修饰。在这篇综述中,我们讨论了 DNA 甲基化、组蛋白修饰和非编码 RNA 在 SSc 中的作用的最新见解,以及这些表观遗传改变如何影响疾病特征。特别是,组蛋白修饰在调节与成纤维细胞向肌成纤维细胞激活相关的基因表达方面发挥作用,决定其命运。DNA 甲基转移酶通过介导特定启动子的 DNA 甲基化,调节特定途径的表达,在疾病发病机制中起着至关重要的作用。我们讨论了针对这些酶的治疗获益。创新的表观遗传学疗法可以针对特定的表观遗传学方法治疗这种疾病。