Migliore Brooke A, Zhou Linran, Duparc Martin, Robles Veronica R, Rehder Catherine W, Peay Holly L, Kucera Katerina S
RTI International, Research Triangle Park, Durham, NC 27709, USA.
Department of Pathology, Duke University, Durham, NC 27710, USA.
Int J Neonatal Screen. 2022 Jan 28;8(1):12. doi: 10.3390/ijns8010012.
Duchenne Muscular Dystrophy (DMD) is a fatal X-linked disorder with a birth prevalence of 19.8:100,000 males worldwide. Elevated concentration of the muscle enzyme creatine kinase-MM (CK-MM) allows for presymptomatic screening of newborns using Dried Blood Spots (DBS). We evaluated imprecision and carryover of the FDA-approved PerkinElmer GSP Neonatal CK-MM kit over multiple runs, days, and operators, followed by quantification of CK-MM loss in stored newborn, contrived, and non-newborn patient DBS resulting from exposure to ambient versus low humidity (50-day trial), and high humidity and high temperature (8-day trial). Imprecision %CV was ≤14% for all verification comparisons and over 6 months of testing. On average, the mean CK-MM recovery after 50 days was >80% of initial concentration for all sample types stored in low humidity and <80% in ambient humidity. After 8 days of storage in high humidity and high temperature, the mean recovery for newborn samples was <80%. Verification results for the GSP Neonatal CK-MM assay were concordant with kit parameters and the assay performed consistently over 6 months. CK-MM degradation in ambient storage can be mitigated by reducing exposure to humidity. Assessment of DBS shipping and storage conditions is recommended prior to implementing DMD screening.
杜氏肌营养不良症(DMD)是一种致命的X连锁疾病,全球男性出生患病率为19.8:100,000。肌肉酶肌酸激酶-MM(CK-MM)浓度升高使得可以使用干血斑(DBS)对新生儿进行症状前筛查。我们评估了经美国食品药品监督管理局(FDA)批准的珀金埃尔默GSP新生儿CK-MM试剂盒在多次运行、多天以及不同操作人员情况下的不精密度和携带污染情况,随后对储存的新生儿、人工合成以及非新生儿患者干血斑中因暴露于环境湿度与低湿度(50天试验)、高湿度和高温(8天试验)导致的CK-MM损失进行了定量分析。在所有验证比较以及超过6个月的测试中,不精密度%CV≤14%。平均而言,在低湿度环境下储存50天后,所有样本类型的CK-MM平均回收率均高于初始浓度的80%,而在环境湿度下则低于80%。在高湿度和高温环境下储存8天后,新生儿样本的平均回收率低于80%。GSP新生儿CK-MM检测的验证结果与试剂盒参数一致,并且该检测在6个月内表现稳定。通过减少湿度暴露可以减轻环境储存中CK-MM的降解。建议在实施DMD筛查之前评估干血斑的运输和储存条件。