Northern Genetics Service, Institute of Genetic Medicine, International Centre for Life, Newcastle Upon Tyne, NE1 3BZ, UK.
Northern Genetics Service, Institute of Genetic Medicine, International Centre for Life, Newcastle Upon Tyne, NE1 3BZ, UK.
Eur J Med Genet. 2022 May;65(5):104491. doi: 10.1016/j.ejmg.2022.104491. Epub 2022 Mar 23.
Hartsfield syndrome is a rare condition characterised by the co-occurrence of ectrodactyly and holoprosencephaly spectrum disorders; cleft lip and palate is a common associated feature. This is due to either monoallelic, or less commonly, biallelic variants in FGFR1 with a loss of function or dominant negative effect. To date 37 individuals have been reported, including two instances of germline mosaicism. We report a further family with Hartsfield syndrome due to a novel variant in FGFR1, with two affected fetuses, and somatic and germline mosaicism in the father detected on Sanger sequencing. The father had not come to medical attention prior to this finding. In light of our findings and those in the published literature, we suggest that mosaicism, either germline or germline and somatic, may be a relatively frequent finding, affecting 3 of 35 (9%) reported families, which has important implications for genetic counselling.
哈特斯菲尔德综合征是一种罕见的疾病,其特征为并指(趾)畸形和前脑无裂畸形谱系障碍同时发生;唇腭裂是常见的相关特征。这归因于 FGFR1 的单等位基因,或较少见的双等位基因变异,表现为功能丧失或显性负效应。迄今为止,已有 37 名个体被报道,包括 2 例种系嵌合体。我们报告了另一个因 FGFR1 中的新型变异而导致的哈特斯菲尔德综合征家族,该家族有两个受影响的胎儿,以及在父亲身上通过 Sanger 测序检测到的体细胞和种系嵌合体。在此发现之前,父亲并未引起医疗关注。鉴于我们的发现和已发表文献中的发现,我们建议嵌合体,无论是种系还是种系和体细胞,可能是一种相对常见的发现,影响了 35 个报告家族中的 3 个(9%),这对遗传咨询具有重要意义。