Patel Ealin N, Turner Lewis D, Hixon Mark S, Janda Kim D
Departments of Chemistry and Immunology, The Skaggs Institute for Chemical Biology, Worm Institute of Research and Medicine (WIRM), The Scripps Research Institute, 10550 North Torrey Pines Road, La Jolla, California 92037, United States.
Biosplice Therapeutics, 9360 Towne Centre Drive, San Diego, California 92121, United States.
ACS Med Chem Lett. 2022 Mar 8;13(4):742-747. doi: 10.1021/acsmedchemlett.2c00028. eCollection 2022 Apr 14.
Botulinum neurotoxin A (BoNT/A) is a lethal toxin, which causes botulism, and is categorized as a bioterrorism threat, which causes flaccid paralysis and death. Botulinum A neurotoxicity is governed through its light chain (LC), a zinc metalloprotease. Pharmacological investigations aimed at negating BoNT/A's LC have typically looked to inhibitors that have been shown to inhibit the light chain's activity by reversible zinc chelation within its active site. This report outlines the first examples of nonpeptidic inhibitors of the BoNT/A LC that possess slow-binding kinetics, a needed logic to counteract the longevity of BoNT/A. Cyclopropane, alkyl, and alkenyl derivatives of 2,4-dichlorocinamic hydroxamic acid (DCHA) were shown to possess both one-step and two-step slow-binding kinetics. Structure-kinetic relationships (SKRs) were observed and were rationalized with the aid of docking models that predicted improved interactions with residues within a hydrophobic cleft adjacent to the active site.
肉毒杆菌神经毒素A(BoNT/A)是一种致命毒素,可导致肉毒中毒,被列为生物恐怖主义威胁因素,会引起弛缓性麻痹和死亡。肉毒杆菌A神经毒性是通过其轻链(LC)来控制的,轻链是一种锌金属蛋白酶。旨在消除BoNT/A轻链的药理学研究通常着眼于那些已被证明可通过在其活性位点内进行可逆的锌螯合来抑制轻链活性的抑制剂。本报告概述了具有慢结合动力学的BoNT/A轻链非肽类抑制剂的首个实例,这是抵消BoNT/A持久性所需的逻辑。2,4 - 二氯肉桂异羟肟酸(DCHA)的环丙烷、烷基和烯基衍生物显示出具有单步和两步慢结合动力学。观察到了结构 - 动力学关系(SKR),并借助对接模型进行了合理化分析,该模型预测与活性位点相邻疏水裂缝内的残基相互作用会得到改善。