Base-edited cynomolgus monkeys mimic core symptoms of STXBP1 encephalopathy.
作者信息
Lu Zongyang, He Siting, Jiang Jian, Zhuang Ling, Wang Yan, Yang Guang, Jiang Xiaoyu, Nie Yanhong, Fu Jiqiang, Zhang Xiaotong, Lu Yong, Bian Xinyan, Chang Hung-Chun, Xiong Zhiqi, Huang Xingxu, Liu Zhen, Sun Qiang
出版信息
Mol Ther. 2022 Aug 3;30(8):2869-2873. doi: 10.1016/j.ymthe.2022.06.020. Epub 2022 Jul 6.
Abstract
摘要
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