Hochman Michael J, Smith B Douglas, Karantanos Theodoros, Braunstein Evan M, Gojo Ivana, Jain Tania, Streiff Michael B, Moliterno Alison R, DeZern Amy E
Division of Hematological Malignancies and Bone Marrow Transplantation, Sidney Kimmel Comprehensive Cancer Center, The Johns Hopkins University School of Medicine, 1650 Orleans Street, CRBI Room 3M87, Baltimore, MD, 21287-0013, USA.
Division of Hematology, Department of Medicine, Johns Hopkins Hospital, Baltimore, MD, USA.
Int J Hematol. 2023 Mar;117(3):456-462. doi: 10.1007/s12185-022-03463-0. Epub 2022 Oct 1.
Myeloproliferative neoplasms (MPN) are chronic clonal disorders characterized by overproduction of myeloid-lineage blood cells and potential risk of evolution to acute myeloid leukemia (AML). Chronic myeloid leukemia (CML) is distinct from other MPNs in that its pathophysiology stems from the BCR-ABL fusion protein of the Philadelphia chromosome (Ph +). Though there are known cases of Ph- and Ph + MPNs coexisting in a single patient, overall prevalence has never been quantified in a prospective cohort. Here, we review our center's MPN registry, which shows 0.6% of Ph- MPN patients later developed CML. This development occurred no less than 10 and up to 36 years after Ph- MPN diagnosis. This rate of chronic transformation exceeds what is expected, as the incidence of CML in the United States is 2 per 100,000 people-years. The probability of this CML case rate in an average-risk population is less than 0.001%, suggesting there are shared risk factors between Ph- and Ph + MPNs. We speculate that these risk factors may include exposures, genetic predispositions, or be inherent to disease biology. Abrupt-onset leukocytosis heralded post-MPN CML in all cases here and suggests this salient clinical feature should trigger hematologists to consider this diagnosis and perform appropriate testing.
骨髓增殖性肿瘤(MPN)是一种慢性克隆性疾病,其特征是髓系血细胞过度生成,并存在演变为急性髓系白血病(AML)的潜在风险。慢性髓系白血病(CML)与其他MPN不同,其病理生理学源于费城染色体(Ph+)的BCR-ABL融合蛋白。虽然已知有单个患者同时存在Ph-和Ph+ MPN的病例,但在前瞻性队列中从未对总体患病率进行过量化。在此,我们回顾了我们中心的MPN登记情况,结果显示0.6%的Ph- MPN患者后来发展为CML。这种情况发生在Ph- MPN诊断后不少于10年且最长达36年。这种慢性转化的发生率超过了预期,因为美国CML的发病率为每10万人年2例。在平均风险人群中出现这种CML病例率的概率小于0.001%,这表明Ph-和Ph+ MPN之间存在共同的风险因素。我们推测这些风险因素可能包括接触因素、遗传易感性或疾病生物学固有的因素。在这里的所有病例中,急性白细胞增多症预示着MPN后CML的发生,这表明这一显著的临床特征应促使血液科医生考虑这一诊断并进行适当的检查。