Department of Hematology, Jewish General Hospital, Montreal, QC H3T 1E2, Canada.
Department of Medicine, Dalhousie University/Nova Scotia Health, Halifax, NS B3H 2Y9, Canada.
Curr Oncol. 2022 Sep 28;29(10):7122-7139. doi: 10.3390/curroncol29100560.
Waldenström macroglobulinemia (WM) is a slowly progressing B-cell non-Hodgkin lymphoma characterized by monoclonal IgM gammopathy in the blood and infiltration of the bone marrow by clonal lymphoplasmacytic cells. As an incurable disease, the goals for therapy for WM are to relieve symptoms, slow disease progression, prevent organ damage, and maintain quality of life. However, given the rarity of WM, clinical trials comparing treatments for WM are limited and there is no definitive standard of care. The selection of first-line WM therapy is thus based on patient factors, disease characteristics, and drug access, with bendamustine-rituximab and Bruton's tyrosine kinase (BTK) inhibitor therapy considered preferred treatments. Other treatments such as proteasome inhibitor- or purine analogue-based therapy, alternative chemoimmunotherapy, and autologous stem cell transplantation are generally reserved for the relapsed setting but may be used in rare circumstances in earlier lines of therapy. This paper summarizes the efficacy and safety of these WM therapies and discusses considerations for treatment from a Canadian perspective.
华氏巨球蛋白血症(WM)是一种进展缓慢的 B 细胞非霍奇金淋巴瘤,其特征是血液中单克隆 IgM 球蛋白血症和克隆性淋巴浆细胞浸润骨髓。作为一种无法治愈的疾病,WM 的治疗目标是缓解症状、减缓疾病进展、预防器官损伤和维持生活质量。然而,由于 WM 的罕见性,比较 WM 治疗的临床试验有限,也没有明确的治疗标准。因此,WM 的一线治疗选择取决于患者因素、疾病特征和药物可及性,苯达莫司汀-利妥昔单抗和布鲁顿酪氨酸激酶(BTK)抑制剂治疗被认为是首选治疗方法。其他治疗方法,如蛋白酶体抑制剂或嘌呤类似物为基础的治疗、替代化疗免疫治疗和自体干细胞移植,通常保留用于复发患者,但在极少数情况下也可用于早期治疗线。本文总结了这些 WM 治疗方法的疗效和安全性,并从加拿大的角度讨论了治疗的注意事项。