Edging closer to successful gene therapy for Wilson disease.
作者信息
Sandahl Thomas Damgaard, Medici Valentina
机构信息
Department of Hepatology and Gastroenterology, Aarhus University Hospital, Aarhus, Denmark.
Department of Internal Medicine, Division of Gastroenterology and Hepatology, University of California Davis, Davis, CA, USA.
出版信息
Mol Ther Methods Clin Dev. 2022 Oct 21;27:293-294. doi: 10.1016/j.omtm.2022.10.005. eCollection 2022 Dec 8.
Abstract
摘要
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