Department of Bioengineering, College of Engineering, BK FOUR Biopharmaceutical Innovation Leader for Education and Research Group, Hanyang University, Seoul 04763, Republic of Korea.
Department of Bioengineering, College of Engineering, BK FOUR Biopharmaceutical Innovation Leader for Education and Research Group, Hanyang University, Seoul 04763, Republic of Korea; Institute of Nano Science and Technology (INST), Institute for Bioengineering and Biopharmaceutical Research (IBBR), Hanyang University, Seoul 04763, Republic of Korea; Elixir Pharmatech Inc., Seoul 07463, Republic of Korea.
J Control Release. 2023 Mar;355:730-744. doi: 10.1016/j.jconrel.2023.02.002. Epub 2023 Feb 22.
Glioblastoma multiforme (GBM) is a central nervous system disease with poor prognosis. Curative treatments for GBM involve chemotherapy, radiotherapy, and surgical pathways. Recently, antiangiogenic therapy through medications has been tried to slow tumor growth, but the drugs can induce side effects. To overcome these limitations, we developed a new orally absorbable form of heparin that can attenuate angiogenic activity by binding to growth factors around the tumor tissue. We conjugated lactoferrin (Lf) to heparin because Lf can be orally absorbed, and it interacts with the lactoferrin receptor (Lf-R) expressed on the intestine, blood-brain barrier (BBB), and glioma tumor masses. We successfully conjugated Lf and heparin by amide bond formation, as evidenced by advanced physicochemical properties such as pharmacokinetics and stability in acidic condition. This new material inhibited angiogenesis in vitro without toxicity. In addition, Lf-heparin administered orally to GBM orthotopic mice was absorbed in the small intestine and delivered specifically to the brain tumor by receptor transcytosis (Lf-R). Lf-heparin further attenuated angiogenesis progression in GBM orthotopic mice. Based on these results, Lf-heparin shows potential as a new oral medication for treatment of glioblastoma.
多形性胶质母细胞瘤(GBM)是一种预后不良的中枢神经系统疾病。GBM 的治疗方法包括化疗、放疗和手术途径。最近,通过药物进行抗血管生成治疗已被尝试用于减缓肿瘤生长,但这些药物会引起副作用。为了克服这些限制,我们开发了一种新的可口服吸收的肝素形式,它可以通过与肿瘤组织周围的生长因子结合来减弱血管生成活性。我们将乳铁蛋白(Lf)与肝素结合,因为 Lf 可以口服吸收,并且它与肠道、血脑屏障(BBB)和神经胶质瘤肿瘤组织上表达的乳铁蛋白受体(Lf-R)相互作用。我们成功地通过酰胺键形成将 Lf 和肝素结合,这可以通过先进的物理化学性质(如药代动力学和在酸性条件下的稳定性)来证明。这种新材料在体外抑制血管生成而没有毒性。此外,Lf-肝素经口服给予 GBM 原位小鼠后,在小肠中被吸收,并通过受体转胞吞作用(Lf-R)特异性递送至脑肿瘤。Lf-肝素进一步减弱了 GBM 原位小鼠的血管生成进展。基于这些结果,Lf-肝素显示出作为治疗神经胶质瘤的新型口服药物的潜力。