Université Paris Cité APHP, Hématologie Greffe, Hôpital Saint Louis; INSERM UMR 976, Hôpital Saint Louis.
EBMT, Statistical Unit, Paris.
Haematologica. 2023 Sep 1;108(9):2369-2379. doi: 10.3324/haematol.2023.282729.
Debates on the role and timing of allogeneic hemtopoietic stem cell transplantation (HSCT) in acute myelogenous leukemia (AML) have persisted for decades. Time to transplant introduces an immortal time and current treatment algorithm mainly relies on the European LeukemiaNet disease risk classification. Previous studies are also limited to age groups, remission status and other ill-defined parameters. We studied all patients at diagnosis irrespective of age and comorbidities to estimate the cumulative incidence and potential benefit or disadvantage of HSCT in a single center. As a time-dependent covariate, HSCT improved overall survival in intermediate- and poor-risk patients (hazard ratio =0.51; P=0.004). In goodrisk patients only eight were transplanted in first complete remission. Overall, the 4-year cumulative incidence of HSCT was only 21.9% but was higher (52.1%) for patients in the first age quartile (16-57 years old) and 26.4% in older patients (57-70 years old) (P<0.001). It was negligible in patients older than 70 years reflecting our own transplant policy but also barriers to transplantation (comorbidities and remission status). However, HSCT patients need to survive, be considered eligible both by the referring and the HSCT physicians and have a suitable donor to get transplantation. We, thus, comprehensively analyzed the complete decision-making and outcome of all our AML patients from diagnosis to last followup to decipher how patient allocation and therapy inform the value of HSCT. The role of HSCT in AML is shifting with broad access to different donors including haploidentical ones. Thus, it may (or may not) lead to increased numbers of allogeneic HSCT in AML in adults.
在急性髓系白血病(AML)中,异体造血干细胞移植(HSCT)的作用和时机一直存在争议,已经持续了几十年。移植时间引入了一个不可逾越的时间,目前的治疗算法主要依赖于欧洲白血病网络疾病风险分类。以前的研究也仅限于年龄组、缓解状态和其他定义不明确的参数。我们研究了所有诊断时的患者,无论年龄和合并症如何,以估计在一个单一中心进行 HSCT 的累积发生率和潜在的益处或弊端。作为一个时变协变量,HSCT 改善了中危和高危患者的总生存率(风险比=0.51;P=0.004)。在低危患者中,只有 8 人在首次完全缓解时进行了 HSCT。总的来说,HSCT 的 4 年累积发生率仅为 21.9%,但在年龄第一四分位数(16-57 岁)的患者中更高(52.1%),在年龄较大的患者(57-70 岁)中为 26.4%(P<0.001)。在 70 岁以上的患者中,这一比例可以忽略不计,这反映了我们自己的移植政策,但也反映了移植的障碍(合并症和缓解状态)。然而,HSCT 患者需要生存,既需要转诊医生,也需要 HSCT 医生认为他们有资格进行移植,并且需要有合适的供体才能进行移植。因此,我们全面分析了从诊断到最后随访的所有 AML 患者的完整决策和结果,以解读患者的分配和治疗如何为 HSCT 的价值提供信息。随着广泛获得包括半相合供体在内的不同供体,HSCT 在 AML 中的作用正在发生转变。因此,它可能(也可能不会)导致成人 AML 中异体 HSCT 的数量增加。