Peking University People's Hospital, Peking University Institute of Hematology, National Clinical Research Center for Hematologic Disease, Beijing Key Laboratory of Hematopoietic Stem Cell Transplantation, Beijing, China.
Department of Hematology, The First Affiliated Hospital of Xinjiang Medical University, Urumqi, China.
Am J Hematol. 2023 Sep;98(9):1394-1406. doi: 10.1002/ajh.26999. Epub 2023 Jun 27.
Chronic myelomonocytic leukemia (CMML) is a clonal hematopoietic stem cell malignancy, and allogeneic hematopoietic stem cell transplantation (allo-HSCT) is the only curable treatment. The outcomes after transplant are influenced by both disease characteristics and patient comorbidities. To develop a novel prognostic model to predict the post-transplant survival of CMML patients, we identified risk factors by applying univariable and multivariable Cox proportional hazards regression to a derivation cohort. In multivariable analysis, advanced age (hazard ratio [HR] 3.583), leukocyte count (HR 3.499), anemia (HR 3.439), bone marrow blast cell count (HR 2.095), and no chronic graft versus host disease (cGVHD; HR 4.799) were independently associated with worse survival. A novel prognostic model termed ABLAG (Age, Blast, Leukocyte, Anemia, cGVHD) was developed and the points were assigned according to the regression equation. The patients were categorized into low risk (0-1), intermediate risk (2, 3), and high risk (4-6) three groups and the 3-year overall survival (OS) were 93.3% (95%CI, 61%-99%), 78.9% (95%CI, 60%-90%), and 51.6% (95%CI, 32%-68%; p < .001), respectively. In internal and external validation cohort, the area under the receiver operating characteristic (ROC) curves of the ABLAG model were 0.829 (95% CI, 0.776-0.902) and 0.749 (95% CI, 0.684-0.854). Compared with existing models designed for the nontransplant setting, calibration plots, and decision curve analysis showed that the ABLAG model revealed a high consistency between predicted and observed outcomes and patients could benefit from this model. In conclusion, combining disease and patient characteristic, the ABLAG model provides better survival stratification for CMML patients receiving allo-HSCT.
慢性粒单核细胞白血病(CMML)是一种克隆性造血干细胞恶性肿瘤,异基因造血干细胞移植(allo-HSCT)是唯一可治愈的治疗方法。移植后的结果受疾病特征和患者合并症的影响。为了开发一种新的预后模型来预测 CMML 患者移植后的生存情况,我们通过应用单变量和多变量 Cox 比例风险回归分析来识别风险因素,从而在一个推导队列中确定风险因素。在多变量分析中,年龄较大(风险比[HR]3.583)、白细胞计数(HR3.499)、贫血(HR3.439)、骨髓原始细胞计数(HR2.095)和无慢性移植物抗宿主病(cGVHD;HR4.799)与生存较差独立相关。提出了一种新的预后模型,称为 ABLAG(年龄、原始细胞、白细胞计数、贫血、cGVHD),并根据回归方程分配分数。患者分为低危(0-1)、中危(2、3)和高危(4-6)三组,3 年总生存率(OS)分别为 93.3%(95%CI,61%-99%)、78.9%(95%CI,60%-90%)和 51.6%(95%CI,32%-68%;p<.001)。在内部和外部验证队列中,ABLAG 模型的接收者操作特征(ROC)曲线下面积分别为 0.829(95%CI,0.776-0.902)和 0.749(95%CI,0.684-0.854)。与为非移植环境设计的现有模型相比,校准图和决策曲线分析表明,ABLAG 模型显示出预测结果与观察结果之间的高度一致性,患者可以从该模型中受益。总之,结合疾病和患者特征,ABLAG 模型为接受 allo-HSCT 的 CMML 患者提供了更好的生存分层。