Takeichi Takuya, Hamada Takahiro, Yamamoto Mayuko, Ito Yasutoshi, Kawaguchi Aya, Kobashi Haruka, Yoshikawa Takenori, Koga Hiroshi, Ishii Norito, Nakama Takekuni, Muro Yoshinao, Ogi Tomoo, Akiyama Masashi
Department of Dermatology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
Department of Dermatology, Kurume University School of Medicine, Kurume, Japan.
J Dermatol. 2024 Jan;51(1):101-105. doi: 10.1111/1346-8138.16967. Epub 2023 Sep 27.
Pathogenic variants in ABCA12 are important causative genetic defects for autosomal recessive congenital ichthyoses (ARCI), which include congenital ichthyosiform erythroderma (CIE), harlequin ichthyosis, and lamellar ichthyosis. In addition, pathogenic variants in ABCA12 are known to cause a localized nevoid form of CIE due to recessive mosaicism. We previously reported siblings who carried an ABCA12 variant but did not show a "congenital" phenotype. They were considered to have pityriasis rubra pilaris (PRP). Here, we present a further patient with ABCA12 variants whose phenotype was not congenital ichthyosis, in an independent family. Notably, these three patients had geographic unaffected areas. Such areas are not usually found in patients with ARCI who have ABCA12 variants, suggesting mild phenotypes for these patients. Interestingly, the histological features of the ichthyotic lesions in these patients resembled those of PRP. All three patients had homozygous pathogenic missense variants in ABCA12. Our findings expand the phenotypic spectrum of patients with ABCA12 variants.
ABCA12基因的致病性变异是常染色体隐性先天性鱼鳞病(ARCI)的重要致病遗传缺陷,ARCI包括先天性鱼鳞病样红皮病(CIE)、丑角样鱼鳞病和板层状鱼鳞病。此外,已知ABCA12基因的致病性变异会因隐性镶嵌现象导致局限性痣样CIE。我们之前报道过携带ABCA12变异但未表现出“先天性”表型的兄弟姐妹。他们被认为患有毛发红糠疹(PRP)。在此,我们在一个独立家庭中展示了另一名患有ABCA12变异且表型并非先天性鱼鳞病的患者。值得注意的是,这三名患者都有未受影响的地图状区域。在携带ABCA12变异的ARCI患者中通常不会出现这样的区域,这表明这些患者的表型较为轻微。有趣的是,这些患者鱼鳞病病变的组织学特征与PRP相似。所有三名患者在ABCA12基因中都有纯合致病性错义变异。我们的研究结果扩展了ABCA12变异患者的表型谱。