Dhaliwal Armaan, Ravi Soumiya
Department of Internal Medicine, University of Arizona College of Medicine, Tucson, USA.
Cureus. 2023 Sep 4;15(9):e44677. doi: 10.7759/cureus.44677. eCollection 2023 Sep.
The utility of CD19-targeted chimeric antigen receptor T-cell (CAR-T cell) therapy in the management of refractory/relapsed B-cell malignancies has increased tremendously in recent times. In addition to cytokine release syndrome (CRS), neurotoxicity, and infections, CAR-T cell patients develop cytopenias, with about 15% of the patients continuing to have severe cytopenias up to three months after treatment. Retrospective reviews have reported the development of myelodysplastic syndrome (MDS) in patients undergoing CAR-T cell therapy. Here, we describe four cases of MDS and/or clonal cytopenias of undetermined significance (CCUS), developing after CAR-T cell therapy. A retrospective review of four patients with relapsed/refractory B-cell lymphomas treated with CD19-directed autologous CAR-T cell was conducted at our institution. The median age was 72.5 years (range 63-76). Three of the four patients had double-hit diffuse large B-cell lymphoma (DLBCL). The median number of lines of therapy before CAR-T cell was three. Only one patient had a prior autologous stem cell transplant (ASCT). The median time to diagnosis of MDS/CCUS from CAR-T cell therapy was three months. Two cases of CCUS diagnosed were at one- and two-month post-CAR-T cell, and two cases of MDS were diagnosed at 10 and 26 months. None of the patients had dysplastic clones before the initiation of CAR-T cell therapy. Only one patient was found to have CCUS-developed CRS post-CAR-T cell requiring treatment with tocilizumab and steroids. Three patients showed complete response, with one showing a very good partial response. All the patients were in remission with no additional therapies post-CAR-T cell. One patient died secondary to COVID-19-related complications. Four patients with prolonged cytopenias were found to have either MDS or CCUS after CAR-T cell therapy. Two CCUS cases underwent bone marrow evaluation early in the course of cytopenias and may develop into MDS, acute myeloid leukemia (AML), or myeloproliferative neoplasm over time. Our retrospective case series review, compared to previous studies, constitutes of patients with no prior clonal hematopoiesis-related cytogenetic abnormalities, fewer lines of therapy, and only one patient with previous hematopoietic stem cell transplantation (HSCT). Based on the upcoming data and our review, a bone marrow biopsy with next-generation sequencing (NGS) is imperative in patients with prolonged cytopenias after CAR-T cell therapy. A diagnosis of CCUS/MDS in these cases can help guide treatment.
近年来,靶向CD19的嵌合抗原受体T细胞(CAR-T细胞)疗法在难治性/复发性B细胞恶性肿瘤治疗中的应用显著增加。除了细胞因子释放综合征(CRS)、神经毒性和感染外,接受CAR-T细胞治疗的患者还会出现血细胞减少,约15%的患者在治疗后三个月仍有严重的血细胞减少。回顾性研究报告了接受CAR-T细胞治疗的患者发生骨髓增生异常综合征(MDS)。在此,我们描述了4例CAR-T细胞治疗后发生的MDS和/或意义未明的克隆性血细胞减少(CCUS)病例。我们机构对4例接受CD19导向的自体CAR-T细胞治疗的复发/难治性B细胞淋巴瘤患者进行了回顾性研究。中位年龄为72.5岁(范围63 - 76岁)。4例患者中有3例患有双打击弥漫性大B细胞淋巴瘤(DLBCL)。CAR-T细胞治疗前的中位治疗线数为3线。只有1例患者曾接受过自体干细胞移植(ASCT)。从CAR-T细胞治疗到诊断为MDS/CCUS的中位时间为3个月。2例CCUS在CAR-T细胞治疗后1个月和2个月确诊,2例MDS在10个月和26个月确诊。在开始CAR-T细胞治疗前,所有患者均无发育异常克隆。只有1例患者在CAR-T细胞治疗后发生CCUS并伴有CRS,需要用托珠单抗和类固醇治疗。3例患者显示完全缓解,1例显示非常好的部分缓解。所有患者在CAR-T细胞治疗后均处于缓解状态,无需额外治疗。1例患者死于COVID-19相关并发症。4例血细胞减少持续时间较长的患者在CAR-T细胞治疗后被发现患有MDS或CCUS。2例CCUS病例在血细胞减少病程早期接受了骨髓评估,随着时间推移可能发展为MDS、急性髓系白血病(AML)或骨髓增殖性肿瘤。与以往研究相比,我们的回顾性病例系列研究纳入的患者既往无克隆性造血相关细胞遗传学异常、治疗线数较少,且只有1例患者曾接受过造血干细胞移植(HSCT)。基于即将获得的数据和我们的研究,对于CAR-T细胞治疗后血细胞减少持续时间较长的患者,进行下一代测序(NGS)的骨髓活检至关重要。在这些病例中诊断CCUS/MDS有助于指导治疗。