Liu Jannel, Angelos Peter, Barhoum Maan, Jain Rajesh
Department of Endocrinology, Diabetes, and Metabolism, University of Chicago Medicine, Chicago, IL 60637, USA.
Department of Endocrine Surgery, University of Chicago Medicine, Chicago, IL 60637, USA.
JCEM Case Rep. 2023 Aug 9;1(4):luad071. doi: 10.1210/jcemcr/luad071. eCollection 2023 Jul.
Pathogenic variants of CYP24A1 are associated with hypercalcemia due to disruptions in the ability of 24-hydroxylase to break down 1,25-dihydroxyvitamin D (1,25-DHVD). A case involving a heterozygous pathogenic variant of CYP24A1 and primary hyperparathyroidism leading to severe hypercalcemia has not been previously reported. A 23-year-old woman presented with fatigue and was found to be hypercalcemic at 13.8 mg/dL [reference range, 8.4-10.2 pg/mL]. Her parathyroid hormone (PTH) was 62 pg/mL [reference range, 19-88 pg/mL] and 1,25-DHVD was elevated to 242.7 pg/mL [reference range, 18-72 pg/mL]. Other laboratory workup was unrevealing. She had a bone scan, whole body CT scan, and thyroid ultrasound that were normal. Her 25-hydroxy-vitamin D to 24,25-dihydroxy-vitamin D ratio was elevated at 25.18 (normal, < 25). Because of concern for primary hyperparathyroidism, she was referred to an endocrine surgeon and underwent a parathyroidectomy with the removal of a 3.5-gram adenoma. Pathology showed a parafibromin-deficient parathyroid neoplasm. Genetic testing demonstrated a heterozygous pathogenic variant in CYP24A1. Three weeks after surgery, PTH was 14 pg/mL (1.48 pmol/L), calcium and 1,25-DHVD normalized. In summary, we report a case where a patient with severe symptomatic hypercalcemia was found to have primary hyperparathyroidism exacerbated by an underlying heterozygous pathogenic variant in CYP24A1.
CYP24A1的致病变体与高钙血症有关,因为24-羟化酶分解1,25-二羟基维生素D(1,25-DHVD)的能力受到破坏。此前尚未报道过涉及CYP24A1杂合致病变体和原发性甲状旁腺功能亢进导致严重高钙血症的病例。一名23岁女性因疲劳就诊,血钙水平为13.8 mg/dL[参考范围,8.4-10.2 pg/mL],发现血钙过高。她的甲状旁腺激素(PTH)为62 pg/mL[参考范围,19-88 pg/mL],1,25-DHVD升高至242.7 pg/mL[参考范围,18-72 pg/mL]。其他实验室检查未发现异常。她进行了骨扫描、全身CT扫描和甲状腺超声检查,结果均正常。她的25-羟基维生素D与24,25-二羟基维生素D的比值升高至25.18(正常,<25)。由于担心原发性甲状旁腺功能亢进,她被转诊给内分泌外科医生,接受了甲状旁腺切除术,切除了一个3.5克的腺瘤。病理显示为副纤维蛋白缺乏的甲状旁腺肿瘤。基因检测显示CYP24A1存在杂合致病变体。术后三周,PTH为14 pg/mL(1.48 pmol/L),钙和1,25-DHVD恢复正常。总之,我们报告了一例严重症状性高钙血症患者,发现其原发性甲状旁腺功能亢进因潜在的CYP24A1杂合致病变体而加重。