Second Propedeutic Department of Internal Medicine, Hippocration Hospital, Aristotle University of Thessaloniki, 54642 Thessaloniki, Greece.
Adult Thalassemia Unit, 2nd Department of Internal Medicine, Aristotle University of Thessaloniki, Hippocration General Hospital, 54642 Thessaloniki, Greece.
Int J Mol Sci. 2023 Nov 13;24(22):16263. doi: 10.3390/ijms242216263.
Hemoglobinopathies, including β-thalassemia and sickle cell disease (SCD), are common genetic blood disorders. Endocrine disorders are frequent manifestations of organ damage observed mainly in patients with β-thalassemia and rarely in SCD. Iron overload, oxidative stress-induced cellular damage, chronic anemia, and HCV infection contribute to the development of endocrinopathies in β-thalassemia. The above factors, combined with vaso-occlusive events and microcirculation defects, are crucial for endocrine dysfunction in SCD patients. These endocrinopathies include diabetes mellitus, hypothyroidism, parathyroid dysfunction, gonadal and growth failure, osteoporosis, and adrenal insufficiency, affecting the quality of life of these patients. Thus, we aim to provide current knowledge and data about the epidemiology, pathogenesis, diagnosis, and management of endocrine disorders in β-thalassemia and SCD. We conducted a comprehensive review of the literature and examined the available data, mostly using the PubMed and Medline search engines for original articles. In the era of precision medicine, more studies investigating the potential role of genetic modifiers in the development of endocrinopathies in hemoglobinopathies are essential.
血红蛋白病,包括β-地中海贫血和镰状细胞病(SCD),是常见的遗传性血液疾病。内分泌疾病是β-地中海贫血患者主要观察到的器官损伤的常见表现,而在 SCD 中则很少见。铁过载、氧化应激诱导的细胞损伤、慢性贫血和 HCV 感染导致β-地中海贫血患者发生内分泌疾病。上述因素,加上血管阻塞事件和微循环缺陷,是 SCD 患者内分泌功能障碍的关键因素。这些内分泌疾病包括糖尿病、甲状腺功能减退症、甲状旁腺功能障碍、性腺和生长障碍、骨质疏松症和肾上腺功能不全,影响这些患者的生活质量。因此,我们旨在提供有关β-地中海贫血和 SCD 中内分泌疾病的流行病学、发病机制、诊断和管理的最新知识和数据。我们对文献进行了全面审查,并检查了现有数据,主要使用 PubMed 和 Medline 搜索引擎查找原始文章。在精准医学时代,需要更多研究来探讨遗传修饰因子在血红蛋白病内分泌疾病发展中的潜在作用。