Keck School of Medicine of University of Southern California, Cancer and Blood Disease Institute at Children's Hospital Los Angeles, Los Angeles, CA.
Division of Biomedical Statistics and Informatics, Department of Neurosurgery, University of California, San Francisco, San Francisco, CA.
J Clin Oncol. 2024 Apr 20;42(12):1340-1343. doi: 10.1200/JCO.23.01084. Epub 2024 Feb 23.
Why, when, and how to consider external control cohorts in pediatric brain tumor clinical trials.
为何、何时以及如何在儿科脑肿瘤临床试验中考虑外部对照队列。