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Supporting the case for a targeted approach for elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with no F508del CFTR variant: further analysis for the French compassionate use programme.

作者信息

Dooney Michael, Saba Tarek

机构信息

Blackpool Teaching Hospitals NHS Foundation Trust, Blackpool Adult Cystic Fibrosis Service, Blackpool Victoria Hospital, Blackpool, UK

Blackpool Teaching Hospitals NHS Foundation Trust, Blackpool Adult Cystic Fibrosis Service, Blackpool Victoria Hospital, Blackpool, UK.

出版信息

Eur Respir J. 2024 Feb 29;63(2). doi: 10.1183/13993003.01392-2023. Print 2024 Feb.

Abstract
摘要

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