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Impact of arginine therapy on kyotorphin in children with sickle cell disease and vaso-occlusive pain.

作者信息

Korman Rawan, Hatabah Dunia, Brown Lou Ann, Harris Frank, Wilkinson Hagar, Rees Chris A, Bakshi Nitya, Archer David R, Dampier Carlton, Morris Claudia R

机构信息

Department of Pediatrics, Emory University School of Medicine, Atlanta, GA.

Children's Healthcare of Atlanta, Atlanta, GA.

出版信息

Blood Adv. 2024 Jun 25;8(12):3267-3271. doi: 10.1182/bloodadvances.2023012209.

DOI:10.1182/bloodadvances.2023012209
PMID:38527291
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC11226964/
Abstract
摘要
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/d44c70368acd/BLOODA_ADV-2023-012209-gr2.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/38d5a0c8ec4f/BLOODA_ADV-2023-012209-ga1.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/0ecee2e736c2/BLOODA_ADV-2023-012209-gr1.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/d44c70368acd/BLOODA_ADV-2023-012209-gr2.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/38d5a0c8ec4f/BLOODA_ADV-2023-012209-ga1.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/0ecee2e736c2/BLOODA_ADV-2023-012209-gr1.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/7f3f/11226964/d44c70368acd/BLOODA_ADV-2023-012209-gr2.jpg

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Am J Hematol. 2025 Jul;100(7):1119-1131. doi: 10.1002/ajh.27692. Epub 2025 Apr 24.

本文引用的文献

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Sickle Cell Disease Treatment with Arginine Therapy (STArT): study protocol for a phase 3 randomized controlled trial.用精氨酸治疗镰状细胞病(STArT):一项 3 期随机对照试验的研究方案。
Trials. 2023 Aug 17;24(1):538. doi: 10.1186/s13063-023-07538-z.
2
Effects of l-arginine supplementation in patients with sickle cell disease: A systematic review and meta-analysis of clinical trials.补充L-精氨酸对镰状细胞病患者的影响:一项临床试验的系统评价和荟萃分析。
Health Sci Rep. 2023 Apr 11;6(4):e1167. doi: 10.1002/hsr2.1167. eCollection 2023 Apr.
3
Amino acid signature during sickle cell pain crisis shows significant alterations related to nitric oxide and energy metabolism.
镰状细胞疼痛危象期间的氨基酸特征显示与一氧化氮和能量代谢相关的显著改变。
Mol Genet Metab. 2022 Sep-Oct;137(1-2):146-152. doi: 10.1016/j.ymgme.2022.08.004. Epub 2022 Aug 20.
4
Arginine Therapy and Cardiopulmonary Hemodynamics in Hospitalized Children with Sickle Cell Anemia: A Prospective, Double-blinded, Randomized Placebo-controlled Clinical Trial.精氨酸治疗与镰状细胞贫血住院儿童的心肺血流动力学:一项前瞻性、双盲、随机安慰剂对照临床试验。
Am J Respir Crit Care Med. 2022 Jul 1;206(1):70-80. doi: 10.1164/rccm.202108-1930OC.
5
Safety of intravenous arginine therapy in children with sickle cell disease hospitalized for vaso-occlusive pain: A randomized placebo-controlled trial in progress.镰状细胞病患儿因血管闭塞性疼痛住院时静脉注射精氨酸治疗的安全性:一项正在进行的随机安慰剂对照试验。
Am J Hematol. 2022 Jan 1;97(1):E21-E24. doi: 10.1002/ajh.26396. Epub 2021 Nov 12.
6
Impact of oral -arginine supplementation on blood pressure dynamics in children with severe sickle cell vaso-occlusive crisis.口服精氨酸补充剂对重度镰状细胞血管闭塞性危象患儿血压动态的影响。
Am J Cardiovasc Dis. 2021 Feb 15;11(1):136-147. eCollection 2021.
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Peptides. 2018 Mar;101:60-68. doi: 10.1016/j.peptides.2017.12.026. Epub 2017 Dec 28.
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Arginine and citrulline for the treatment of MELAS syndrome.精氨酸和瓜氨酸用于治疗线粒体脑肌病伴乳酸血症和卒中样发作综合征
J Inborn Errors Metab Screen. 2017 Jan;5. doi: 10.1177/2326409817697399. Epub 2017 Mar 24.