Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Surgeons in Ireland, Dublin, Ireland.
Department of Hematology, Erasmus Medical Center, Rotterdam, The Netherlands.
Blood Adv. 2024 Jun 25;8(12):3254-3266. doi: 10.1182/bloodadvances.2023012499.
von Willebrand factor (VWF) undergoes complex posttranslational modification within endothelial cells (ECs) before secretion. This includes significant N- and O-linked glycosylation. Previous studies have demonstrated that changes in N-linked glycan structures significantly influence VWF biosynthesis. In contrast, although abnormalities in VWF O-linked glycans (OLGs) have been associated with enhanced VWF clearance, their effect on VWF biosynthesis remains poorly explored. Herein, we report a novel role for OLG determinants in regulating VWF biosynthesis and trafficking within ECs. We demonstrate that alterations in OLGs (notably reduced terminal sialylation) lead to activation of the A1 domain of VWF within EC. In the presence of altered OLG, VWF multimerization is reduced and Weibel-Palade body (WPB) formation significantly impaired. Consistently, the amount of VWF secreted from WPB after EC activation was significantly reduced in the context of O-glycosylation inhibition. Finally, altered OLG on VWF not only reduced the amount of VWF secreted after EC activation but also affected its hemostatic efficacy. Notably, VWF secreted after WPB exocytosis consisted predominantly of low molecular weight multimers, and the length of tethered VWF string formation on the surface of activated ECs was significantly reduced. In conclusion, our data therefore support the hypothesis that alterations in O-glycosylation pathways directly affect VWF trafficking within human EC. These findings are interesting given that previous studies have reported altered OLG on plasma VWF (notably increased T-antigen expression) in patients with von Willebrand disease.
血管性血友病因子(VWF)在分泌前在内皮细胞(ECs)中经历复杂的翻译后修饰。这包括大量的 N-和 O-连接糖基化。以前的研究表明,N-连接聚糖结构的变化显著影响 VWF 的生物合成。相比之下,尽管 VWF O-连接聚糖(OLG)的异常与增强的 VWF 清除有关,但它们对 VWF 生物合成的影响仍未得到充分探索。在此,我们报告了 OLG 决定因素在调节内皮细胞内 VWF 生物合成和运输中的新作用。我们证明,OLG 的改变(特别是末端唾液酸化减少)导致内皮细胞内 VWF A1 结构域的激活。在改变的 OLG 存在下,VWF 多聚化减少,Weibel-Palade 体(WPB)形成显著受损。一致地,在 O-糖基化抑制的情况下,从 WPB 分泌的 VWF 量在 OLG 改变的情况下显著减少。最后,改变的 VWF OLG 不仅减少了 EC 激活后分泌的 VWF 量,而且还影响了其止血功效。值得注意的是,WPB 胞吐后分泌的 VWF 主要由低分子量多聚体组成,并且在激活的 EC 表面上连接的 VWF 字符串形成的长度显著减少。总之,我们的数据因此支持这样一种假设,即 O-糖基化途径的改变直接影响人 EC 内的 VWF 运输。这些发现很有趣,因为以前的研究报告了血管性血友病患者血浆 VWF 上的 OLG 改变(特别是 T 抗原表达增加)。