Yen Angela, Zappala Zachary, Fine Rebecca S, Majarian Timothy D, Sripakdeevong Parin, Altshuler David
Vertex Pharmaceuticals, Boston, MA.
CRISPR Therapeutics, Boston, MA.
N Engl J Med. 2024 May 9;390(18):1723-1725. doi: 10.1056/NEJMc2313119. Epub 2024 Apr 24.