Division of Allergy, Immunology, and Rheumatology, University of Rochester Medical Center, 601 Elmwood Ave, Box 695, Rochester, NY 14642, USA.
Int J Mol Sci. 2024 Apr 26;25(9):4728. doi: 10.3390/ijms25094728.
Systemic sclerosis (SSc) is a heterogeneous disease characterized by autoimmunity, vasculopathy, and fibrosis which affects the skin and internal organs. One key aspect of SSc vasculopathy is pulmonary arterial hypertension (SSc-PAH) which represents a leading cause of morbidity and mortality in patients with SSc. The pathogenesis of pulmonary hypertension is complex, with multiple vascular cell types, inflammation, and intracellular signaling pathways contributing to vascular pathology and remodeling. In this review, we focus on shared molecular features of pulmonary hypertension and those which make SSc-PAH a unique entity. We highlight advances in the understanding of the clinical and translational science pertinent to this disease. We first review clinical presentations and phenotypes, pathology, and novel biomarkers, and then highlight relevant animal models, key cellular and molecular pathways in pathogenesis, and explore emerging treatment strategies in SSc-PAH.
系统性硬化症(SSc)是一种异质性疾病,其特征为自身免疫、血管病变和纤维化,影响皮肤和内脏器官。SSc 血管病变的一个关键方面是肺动脉高压(SSc-PAH),这是 SSc 患者发病率和死亡率的主要原因。肺动脉高压的发病机制很复杂,多种血管细胞类型、炎症和细胞内信号通路导致血管病变和重塑。在这篇综述中,我们重点关注肺动脉高压的共同分子特征以及使 SSc-PAH 成为独特实体的特征。我们强调了对与该疾病相关的临床和转化科学的理解的进展。我们首先回顾临床表现和表型、病理学和新型生物标志物,然后重点介绍相关的动物模型、发病机制中的关键细胞和分子途径,并探讨 SSc-PAH 中新兴的治疗策略。