Department of Haematology, Singapore General Hospital, Singapore.
Department of Haematology, National Cancer Centre Singapore, Singapore.
Ann Acad Med Singap. 2023 Nov 29;52(11):601-624. doi: 10.47102/annals-acadmedsg.2023101.
AL amyloidosis is the most common form of systemic amyloidosis. However, the non-specific nature of presenting symptoms requires the need for a heightened clinical suspicion to detect unexplained manifestations in the appropriate clinical setting. Early detection and treatment are crucial as the degree of cardiac involvement emerges as a primary prognostic predictor of survival in a patient with AL amyloidosis. Following the diagnosis of AL amyloidosis with appropriate tissue biopsies, prompt treatment with a bortezomib, cyclophosphamide and dexamethasone-based first-line induction with or without daratumumab should be initiated. The goal of treatment is to achieve the best haematologic response possible, ideally with involved free light chain <20 mg/L, as it offers the best chance of organ function improvement. Treatment should be changed if patients do not achieve a partial response within 2 cycles of treatment or very good partial response after 4 cycles or after autologous stem cell transplant, as achievement of profound and prolonged clonal responses translates to better organ response and long-term outcomes. Early involvement of multidisciplinary subspecialists such as renal physicians, cardiologists, neurologists, and gastroenterologists for optimal maintenance and support of involved organs is recommended for optimal management of patients with AL amyloidosis.
AL 淀粉样变是最常见的系统性淀粉样变。然而,由于其临床表现无特异性,需要高度的临床怀疑,以便在适当的临床环境中发现不明原因的表现。早期发现和治疗至关重要,因为心脏受累的程度是 AL 淀粉样变患者生存的主要预后预测因素。在通过适当的组织活检诊断出 AL 淀粉样变后,应立即启动硼替佐米、环磷酰胺和地塞米松为基础的一线诱导治疗,联合或不联合达雷妥尤单抗。治疗的目标是尽可能达到最佳的血液学缓解,理想情况下游离轻链<20mg/L,因为这提供了改善器官功能的最佳机会。如果患者在 2 个疗程内未达到部分缓解,或在 4 个疗程或自体干细胞移植后达到非常好的部分缓解,应更换治疗方案,因为达到深度和持久的克隆反应可转化为更好的器官反应和长期结局。建议多学科专家(如肾内科医生、心脏病专家、神经科医生和胃肠病专家)尽早参与,以优化受累器官的维持和支持,从而优化 AL 淀粉样变患者的管理。