Regulatory Affairs, Simulations Plus Inc., 42505 10th Street West, Lancaster, California 93534-7059, United States.
Janssen Pharmaceutica NV, Turnhoutseweg 30, 2340 Beerse, Belgium.
Mol Pharm. 2024 Aug 5;21(8):3697-3731. doi: 10.1021/acs.molpharmaceut.4c00526. Epub 2024 Jun 30.
This Article shares the proceedings from the August 29th, 2023 (day 1) workshop "Physiologically Based Biopharmaceutics Modeling (PBBM) Best Practices for Drug Product Quality: Regulatory and Industry Perspectives". The focus of the day was on model parametrization; regulatory authorities from Canada, the USA, Sweden, Belgium, and Norway presented their views on PBBM case studies submitted by industry members of the IQ consortium. The presentations shared key questions raised by regulators during the mock exercise, regarding the PBBM input parameters and their justification. These presentations also shed light on the regulatory assessment processes, content, and format requirements for future PBBM regulatory submissions. In addition, the day 1 breakout presentations and discussions gave the opportunity to share best practices around key questions faced by scientists when parametrizing PBBMs. Key questions included measurement and integration of drug substance solubility for crystalline vs amorphous drugs; impact of excipients on apparent drug solubility/supersaturation; modeling of acid-base reactions at the surface of the dissolving drug; choice of dissolution methods according to the formulation and drug properties with a view to predict the in vivo performance; mechanistic modeling of in vitro product dissolution data to predict in vivo dissolution for various patient populations/species; best practices for characterization of drug precipitation from simple or complex formulations and integration of the data in PBBM; incorporation of drug permeability into PBBM for various routes of uptake and prediction of permeability along the GI tract.
本文分享了 2023 年 8 月 29 日(第 1 天)研讨会“基于生理学的生物药剂学建模(PBBM)用于药物产品质量的最佳实践:监管和行业视角”的会议记录。会议的重点是模型参数化;来自加拿大、美国、瑞典、比利时和挪威的监管机构介绍了他们对 IQ 联盟行业成员提交的 PBBM 案例研究的看法。演讲分享了监管机构在模拟演练中提出的关于 PBBM 输入参数及其合理性的关键问题。这些演讲还阐明了未来 PBBM 监管提交的监管评估流程、内容和格式要求。此外,第 1 天的分组演示和讨论提供了分享科学家在对 PBBM 进行参数化时面临的关键问题的最佳实践的机会。关键问题包括:结晶和无定形药物的药物物质溶解度的测量和整合;赋形剂对表观药物溶解度/过饱和度的影响;溶解药物表面的酸碱反应建模;根据配方和药物性质选择溶解方法,以预测体内性能;根据各种患者群体/物种的体内溶解数据对体外产品溶解数据进行机制建模;用于简单或复杂配方的药物沉淀特性的最佳实践以及将数据整合到 PBBM 中;将药物渗透性纳入 PBBM 中,用于各种吸收途径,并预测胃肠道中的渗透性。